VX-993 for Pain

MI
Overseen ByMedical Information
Age: 18 - 65
Sex: Male
Trial Phase: Phase 1
Sponsor: Vertex Pharmaceuticals Incorporated
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial explores how the body processes a new pain treatment, 14C-VX-993, after oral administration. Researchers aim to understand how the body absorbs, metabolizes, and eliminates this treatment. They seek participants who weigh more than 50 kg, have a BMI between 18 and 32, and experience at least one regular bowel movement daily. As a Phase 1 trial, the research focuses on understanding how the treatment works in people, offering participants the opportunity to be among the first to receive this new treatment.

Will I have to stop taking my current medications?

The trial information does not specify whether you need to stop taking your current medications. It's best to discuss this with the trial coordinators or your doctor.

Is there any evidence suggesting that this treatment is likely to be safe for humans?

Research has shown that VX-993 was generally safe and well tolerated in earlier studies. Most side effects were mild to moderate, indicating they weren't severe. No serious safety issues emerged, suggesting the treatment is likely safe based on past research. However, as this is a Phase 1 trial, the study remains in the early stages. This phase primarily examines how the body handles the drug, including its safety and how the body absorbs, distributes, and eliminates it.12345

Why do researchers think this study treatment might be promising?

Unlike the standard pain relief options such as NSAIDs, opioids, and acetaminophen, 14C-VX-993 is unique because it introduces a novel active ingredient with a potentially new mechanism of action. Researchers are excited about this treatment as it could offer an alternative pathway for pain management, possibly reducing the reliance on traditional painkillers that often come with significant side effects or risk of dependency. Additionally, the single oral dose administration after fasting may improve patient compliance and streamline the treatment process, making it a promising candidate for future pain management strategies.

What evidence suggests that 14C-VX-993 might be an effective treatment for pain?

Research has shown that VX-993 has not been effective in treating sudden pain. In earlier studies, VX-993 did not outperform current pain treatments or even a placebo, which contains no active medicine. The drug targets a protein called NaV1.8, involved in sending pain signals, but it did not reduce pain more effectively than common painkillers like hydrocodone. Due to these results, the development of VX-993 for sudden pain was halted. In this trial, participants will receive a single oral dose of 14C-VX-993 to study how the body processes the drug, but its ability to relieve pain remains unproven.23678

Are You a Good Fit for This Trial?

This trial is for individuals over 50 kg with a BMI of 18.0 to 32.0 who have at least one regular bowel movement daily. It's not specified who can't join, but typically those with health conditions affecting drug processing or conflicting medications would be excluded.

Inclusion Criteria

I have at least one bowel movement every day.
My BMI is between 18.0 and 32.0.
I weigh more than 50 kg.

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

1-2 weeks

Treatment

Participants receive a single oral dose of 14C-VX-993 after an overnight fast

1 day

Follow-up

Participants are monitored for safety and effectiveness after treatment

2-4 weeks

What Are the Treatments Tested in This Trial?

Interventions

  • 14C-VX-993
Trial Overview The study is testing how the body processes and eliminates a single oral dose of a pain medication called 14C-VX-993 by tracking its radioactivity in the body and understanding its pharmacokinetics (how the drug moves inside the body).
How Is the Trial Designed?
1Treatment groups
Experimental Treatment
Group I: 14C VX-993Experimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Vertex Pharmaceuticals Incorporated

Lead Sponsor

Trials
267
Recruited
36,100+
Dr. David Altshuler profile image

Dr. David Altshuler

Vertex Pharmaceuticals Incorporated

Chief Medical Officer since 2020

MD, PhD

Dr. Reshma Kewalramani profile image

Dr. Reshma Kewalramani

Vertex Pharmaceuticals Incorporated

Chief Executive Officer since 2020

MD, trained in internal medicine and nephrology

Published Research Related to This Trial

Pharmacogenomics (PGx) testing can enhance pain management by allowing for more precise selection and dosing of analgesics based on individual genetic responses, which is crucial given the variability in how patients respond to pain medications.
The Clinical Pharmacogenetics Implementation Consortium (CPIC) provides guidelines that can help healthcare providers apply PGx data in clinical practice, particularly for patients with cancer, to improve the efficacy and safety of pain pharmacotherapy.
Integrating pharmacogenomics into precision pain management.Bates, J., Fudin, J., Patel, JN.[2022]
QX-314, a derivative of lidocaine, selectively inhibits nociceptors expressing TRPV1 channels but may cause central nervous system (CNS) toxicities that are about twice as potent as lidocaine.
In newborn rat brainstem-spinal cord preparations, QX-314 decreased respiratory rhythm generation, indicating potential risks for respiratory function when used systemically.
Effects of a quaternary lidocaine derivative, QX-314, on the respiratory activity in brainstem-spinal cord preparation from newborn rats.Takahashi, K., Hayakawa, C., Onimaru, H.[2016]
VX-128, a selective Nav 1.8 inhibitor, was found to be well-tolerated in single doses up to 300 mg, but showed a higher incidence of adverse effects compared to placebo, with 41.7% of subjects experiencing side effects.
In a multiple-ascending dose study, skin rashes and one serious case of angioedema were reported, leading to early termination of the study, although VX-128 demonstrated a dose-dependent trend in increasing pain tolerance in certain pain tests.
A phase I, randomized, double-blind, placebo-controlled, single- and multiple dose escalation study evaluating the safety, pharmacokinetics and pharmacodynamics of VX-128, a highly selective Nav 1.8 inhibitor, in healthy adults.Hijma, HJ., van Brummelen, EMJ., Siebenga, PS., et al.[2022]

Citations

Vertex Announces Results from Phase 2 Study of VX-993 ...Treatment with VX-993 did not result in a statistically significant improvement on the primary endpoint of the time-weighted Sum of the Pain ...
Evaluation of Efficacy and Safety of VX-993 for Pain ...The date on which the last participant in a clinical study was examined or received an intervention to collect final data for the primary outcome measure.
Vertex's Selective NaV1.8 Inhibitor Falls Short in Acute ...VX-993 failed to demonstrate superior efficacy over existing NaV1. · The trial showed that hydrocodone bitartrate/acetaminophen provided more ...
NaV1.8 Pain Signal Inhibitor VX-993 Fails to Show Efficacy ...Vertex Pharmaceuticals halts VX-993 development for acute pain after phase 2 trial shows no significant efficacy compared with placebo.
A Study to Evaluate How the Body Processes 14C-VX-993 ...The purpose of the study is to evaluate the routes and rate of elimination and recovery of total radioactivity (TRA) and characterize the Pharmac...
A Study to Evaluate How the Body Processes 14C-VX-993 ...The purpose of the study is to evaluate the routes and rate of elimination and recovery of total radioactivity (TRA) and characterize the Pharmacokinetic (PK) ...
A Study to Evaluate How the Body Processes 14C-VX-993 ...The purpose of the study is to evaluate the routes and rate of elimination and recovery of total radioactivity (TRA) and characterize the ...
VX-993 - Drug Targets, Indications, PatentsDespite the setback, VX-993 was found generally safe, with mostly mild to moderate side effects and no serious safety signals. Analysts and investors, who had ...
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