Deep Brain Stimulation for Ataxia

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JC
Overseen ByJulia C Gonzalez, BA
Age: 18+
Sex: Any
Trial Phase: Academic
Sponsor: University of Florida
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial explores a new treatment for spinocerebellar ataxia type 6 (SCA6), a condition affecting balance and coordination. The treatment, Interposed Nucleus aDBS, involves implanting a device in the brain that adjusts its activity based on brain function, aiming to improve symptoms. Individuals diagnosed with SCA6, who have a positive genetic test for it, and can walk with or without support might be suitable candidates for this study. As an unphased trial, this study offers a unique opportunity to contribute to groundbreaking research that could lead to new treatment options.

Do I need to stop taking my current medications for the trial?

The trial information does not specify whether you need to stop taking your current medications. It's best to discuss this with the study team to get a clear answer.

What prior data suggests that cerebellar adaptive deep brain stimulation (aDBS) is safe for adults with spinocerebellar ataxia type 6 (SCA6)?

Research has shown that deep brain stimulation (DBS) is generally safe and well-tolerated for treating cerebellar tremor, based on studies with small patient groups. In these studies, patients reported no major safety issues, and any common side effects were minor.

Adaptive deep brain stimulation (aDBS) enhances this by automatically adjusting stimulation based on brain activity. Since aDBS builds on the established DBS method, it is expected to be equally safe. However, because aDBS is newer, ongoing studies closely monitor participants to ensure safety and manage any side effects. Participants in these studies assist researchers in confirming the safety of this new treatment for ataxia.12345

Why are researchers excited about this trial?

Researchers are excited about Adaptive Deep Brain Stimulation (aDBS) for ataxia because it offers a new way to automatically adjust stimulation levels in the brain based on real-time neural activity. Unlike traditional DBS, which uses fixed settings, aDBS dynamically tunes the stimulation to better match the brain's needs, potentially improving symptom control and reducing side effects. This personalized approach could lead to more effective and safer management of ataxia symptoms compared to existing treatments.

What evidence suggests that adaptive deep brain stimulation is effective for spinocerebellar ataxia type 6?

Research has shown that deep brain stimulation (DBS) might help with movement problems in people with cerebellar ataxias. Early studies suggest that low-frequency DBS can improve these movement issues. This trial will specifically evaluate Adaptive Deep Brain Stimulation (aDBS), which automatically adjusts stimulation amplitude based on recorded neural activity. This treatment sends electrical signals to specific brain parts to help control movement. Evidence indicates that DBS can change brain cell activity, potentially leading to better movement control. While more research is needed, these early findings are promising for people with spinocerebellar ataxia type 6 (SCA6).12467

Who Is on the Research Team?

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Coralie de Hemptinne, PhD

Principal Investigator

University of Florida

Are You a Good Fit for This Trial?

This trial is for adults with a specific type of movement disorder called spinocerebellar ataxia type 6 (SCA6). Participants will be part of a small group, only 5 people, to test the safety and potential benefits of a new treatment involving brain stimulation.

Inclusion Criteria

I have tested positive for SCA6.
Ability to give informed consent for the study
Ability to understand the study protocol
See 4 more

Exclusion Criteria

Severe cognitive impairment or dementia, defined as a score <21 on the Montreal Cognitive Assessment (MOCA)
My ataxia is not caused by SCA6 but may be due to another condition.
I do not have any bleeding disorders, uncontrolled seizures, or conditions that increase my risk for surgery.
See 8 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Surgical Implantation

Participants undergo surgical implantation of DBS leads targeting the motor interposed nucleus of the cerebellum

1 month
1 visit (in-person)

Conventional DBS Programming

Participants begin conventional DBS programming to identify optimal stimulation parameters

8 months
Multiple visits (in-person)

Adaptive DBS Implementation

Transition to adaptive DBS where stimulation amplitude is automatically adjusted based on recorded neural activity

15 months
Multiple visits (in-person)

Follow-up

Participants are monitored for safety and effectiveness after treatment

24 months
18 visits (in-person)

What Are the Treatments Tested in This Trial?

Interventions

  • Interposed Nucleus aDBS

Trial Overview

The study tests cerebellar adaptive deep brain stimulation (aDBS), where surgical implants in the brain help control movement. Over two years, participants will visit the clinic up to 18 times for adjustments and monitoring how well the treatment works.

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: Adaptive Deep Brain Stimulation (aDBS)Experimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

University of Florida

Lead Sponsor

Trials
1,428
Recruited
987,000+

Raynor Cerebellum Project

Collaborator

Citations

NCT07325487 | Interposed Nucleus aDBS for Ataxia

Study outcomes will include assessments of safety and feasibility of cerebellar aDBS, as well as preliminary evaluation of its effects on ...

Interposed Nucleus aDBS for Ataxia - ClinicalTrials.Veeva

Clinical outcomes, symptoms, and potential side effects will be assessed throughout the study using participant self-reports, validated clinical ...

Deep cerebellar stimulation reduces ataxic motor ...

Low-frequency deep cerebellar stimulation may provide a novel strategy for treating motor symptoms of degenerative cerebellar ataxias.

Cerebellar deep brain stimulation rescues Purkinje cell ...

There is evidence that DBS may also be effective in ataxia. It is not known why DBS is effective, but modulating cell activity and conferring ...

Deep Brain Stimulation for Ataxia · Info for Participants

The study tests cerebellar adaptive deep brain stimulation (aDBS), where surgical implants in the brain help control movement. Over two years, ...

6.

pubmed.ncbi.nlm.nih.gov

pubmed.ncbi.nlm.nih.gov/34480330/

Safety and Outcomes of Dentate Nucleus Deep Brain ...

DN DBS is a safe and well tolerated procedure that is effective in alleviating cerebellar tremor. In this small cohort of ataxic patients, DN ...

Real‐time field‐programmable gate array‐based closed‐ ...

Our results confirm the superiority of FPGA-based closed-loop DCN-DBS for alleviating cerebellar ataxia. This evidence supports the ...