This trial is studying safety, how a drug is absorbed and how it affects biomarkers in kids with Duchenne muscular dystrophy. It will be done in two parts.
- Duchenne Muscular Dystrophy
2 Primary · 20 Secondary · Reporting Duration: 12 months
3 Treatment Groups
1 of 3
1 of 3
1 of 3
27 Total Participants · 3 Treatment Groups
Primary Treatment: Cohort 2 · Has Placebo Group · Phase 2
Who is running the clinical trial?
Age 4 - 9 · Male Participants · 4 Total Inclusion CriteriaMark “Yes” if the following statements are true for you:
Frequently Asked Questions
Does this research involve volunteers who are below the age of twenty?
"This trial seeks patients ranging from 4 to 9 years old." - Anonymous Online Contributor
How safe is Cohort 2 for human participants?
"The safety of Cohort 2 scored a 2 on our scale, as there is evidence that it is safe to use but no data yet demonstrating its efficacy." - Anonymous Online Contributor
Are there any open positions available to participants in this investigation?
"The public records on clinicaltrials.gov confirm that this particular medical trial is actively seeking participants, with the first posting having been made on October 1st 2022 and its most recent update occurring in late-October of the same year." - Anonymous Online Contributor
What goals is this trial aiming to accomplish?
"The main aim of the trial, which will be monitored over 12 months, is to assess severity of any adverse events resulting from EDG-5506 and placebo. Additionally, secondary objectives for this experiment include observing changes in neurological examinations among all participants as well as alterations in fast skeletal muscle troponin I levels and coagulation records across all patients." - Anonymous Online Contributor
Which individuals would be ideal candidates for this clinical trial?
"To qualify for this trial, participants must meet the criteria of having muscular dystrophy (Duchenne) and should be between 4 to 9 years old. The study is currently searching for 27 enrollees." - Anonymous Online Contributor
What is the upper limit of participants in this medical research study?
"Indeed, the official data posted on clinicaltrials.gov attests to this experiment's active recruitment process. It was first listed on October 1st 2022 and recently updated on October 24th of the same year. The trial aims to enrol 27 patients from a single site." - Anonymous Online Contributor