Ziftomenib + Mezigdomide for Acute Myeloid Leukemia

Not yet recruiting at 1 trial location
AF
Overseen ByAmir Fathi, MD
Age: Any Age
Sex: Any
Trial Phase: Phase 1
Sponsor: Massachusetts General Hospital
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

The purpose of this study is to evaluate the safety and tolerability of mezigdomide in combination with ziftomenib in adolescent and adult participants with either KMT2A-rearranged (KMT2A-r) or NPM1-mutant relapsed or refractory acute myeloid leukemia (AML).

Who Is on the Research Team?

AF

Amir Fathi, MD

Principal Investigator

Massachusetts General Hospital

Are You a Good Fit for This Trial?

This trial is for adolescents and adults with relapsed or refractory acute myeloid leukemia (AML), specifically those with KMT2A rearrangements or NPM1 mutations. Participants must be over 12 years old, weigh at least 40 kg, have an ECOG performance status of 0-2, and meet certain health criteria including normal liver function tests and a cardiac LVEF of ≥40%.

Inclusion Criteria

I am 16 or older and weigh at least 40 kg.
I am mostly active and can care for myself despite my illness.
My white blood cell count is below 25,000/mcL.
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Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive ziftomenib and mezigdomide orally once daily for 12 cycles

12 cycles (each cycle is 28 days)

Follow-up

Participants are monitored for safety and effectiveness after treatment

Up to 12 months

What Are the Treatments Tested in This Trial?

Interventions

  • Mezigdomide
  • Ziftomenib

Trial Overview

The study is testing the safety and effectiveness of combining two drugs: Ziftomenib and Mezigdomide. It targets patients whose AML has specific genetic changes (KMT2A-r or NPM1-mutant) that have not responded to previous treatments.

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: Ziftomenib and MezigdomideExperimental Treatment2 Interventions

Find a Clinic Near You

Who Is Running the Clinical Trial?

Massachusetts General Hospital

Lead Sponsor

Trials
3,066
Recruited
13,430,000+

Kura Oncology, Inc.

Industry Sponsor

Trials
19
Recruited
1,700+

Bristol-Myers Squibb

Industry Sponsor

Trials
2,731
Recruited
4,127,000+
Headquarters
New York City, USA
Known For
Oncology & Cardiovascular
Top Products
Eliquis, Opdivo, Revlimid, Orencia
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Christopher Boerner

Bristol-Myers Squibb

Chief Executive Officer since 2023

PhD in Business Administration from the Haas School of Business, University of California, Berkeley; BA in Economics and History from Washington University in St. Louis

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Deepak L. Bhatt

Bristol-Myers Squibb

Chief Medical Officer since 2024

MD from Yale University; MSc in Clinical Epidemiology from the University of Pennsylvania