Sulforaphane for Fragile X Tremor/Ataxia Syndrome

Phase-Based Progress Estimates
1
Effectiveness
1
Safety
UC Davis MIND Institute, Sacramento, CAFragile X Tremor/Ataxia SyndromeSulforaphane - DietarySupplement
Eligibility
50 - 85
All Sexes
What conditions do you have?
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Study Summary

This trial is testing a dietary supplement called Sulforaphane to see if it affects specific biomolecular markers captured in blood. Participants take increasing doses of the supplement over 6 months and have 3 medical evaluations.

Eligible Conditions
  • Fragile X Associated Tremor/Ataxia Syndrome (FXTAS)

Treatment Effectiveness

Effectiveness Progress

1 of 3

Similar Trials

Study Objectives

5 Primary · 18 Secondary · Reporting Duration: Baseline, 6 months

Baseline
Changes in cognitive ability
Baseline, 6 months
Changes in FLAIR hypersensitivity volume for subcortical lesions
Changes in Grip Strength
Changes in Hippocampus-mediated memory deficits
Changes in Neurological Quality of Life using the Neuro-QoL lower extremity functioning mobility scale
Changes in Neurological Quality of Life using the Neuro-QoL upper extremity function fine motor scale
Changes in clinical staging of FXTAS
Changes in cognitive dysfunction using MMSE
Changes in cognitive dysfunction using MoCA
Changes in dexterity, tremor, and bradykinesia abnormalities
Changes in executive function deficits using BDS-2
Changes in executive function deficits using COWAT
Changes in frontal executive planning
Changes in gait variability
Changes in kinetic, postural, and rest tremor upper extremity bradykinesia, hypokinesia, dysrhythmia, and dyskinesias
Changes in mitochondrial function via ATP production
Changes in mitochondrial function via mitochondrial membrane potential and mass.
Changes in motor movements
Changes in psychological Issues
Changes in subcortical brain structures damaged in FXTAS through MRI imaging
Observing changes in candidate molecular biomarkers in FXTAS and mitochondrial dysregulation: GRP78
baseline, 6 months
Observing changes in candidate molecular biomarkers in FXTAS and mitochondrial dysregulation: Bax/Bcl-2 ratio
Observing changes in candidate molecular biomarkers in FXTAS and mitochondrial dysregulation: CHOP level

Trial Safety

Safety Progress

1 of 3

Similar Trials

Side Effects for

Sulpforaphane
35%Nausea
35%Flatulence
20%Bloating
20%Diarrhea
20%Dyspepsia
15%Gatrointestinal pain
This histogram enumerates side effects from a completed 2013 Phase 2 trial (NCT01228084) in the Sulpforaphane ARM group. Side effects include: Nausea with 35%, Flatulence with 35%, Bloating with 20%, Diarrhea with 20%, Dyspepsia with 20%.

Trial Design

6 Treatment Groups

Sulforaphane 2 Tablets
1 of 6
Sulforaphane 4 Tablets
1 of 6
Sulforaphane 5 Tablets
1 of 6
Sulforaphane 1 Tablet
1 of 6
Sulforaphane
1 of 6
Sulforaphane 3 Tablets
1 of 6

Experimental Treatment

15 Total Participants · 6 Treatment Groups

Primary Treatment: Sulforaphane · No Placebo Group · N/A

Sulforaphane 2 Tablets
DietarySupplement
Experimental Group · 1 Intervention: Sulforaphane · Intervention Types: DietarySupplement
Sulforaphane 4 Tablets
DietarySupplement
Experimental Group · 1 Intervention: Sulforaphane · Intervention Types: DietarySupplement
Sulforaphane 5 Tablets
DietarySupplement
Experimental Group · 1 Intervention: Sulforaphane · Intervention Types: DietarySupplement
Sulforaphane 1 Tablet
DietarySupplement
Experimental Group · 1 Intervention: Sulforaphane · Intervention Types: DietarySupplement
Sulforaphane
DietarySupplement
Experimental Group · 1 Intervention: Sulforaphane · Intervention Types: DietarySupplement
Sulforaphane 3 Tablets
DietarySupplement
Experimental Group · 1 Intervention: Sulforaphane · Intervention Types: DietarySupplement
Treatment
First Studied
Drug Approval Stage
How many patients have taken this drug
Sulforaphane
2016
Completed Phase 3
~330

Trial Logistics

Trial Timeline

Screening: ~3 weeks
Treatment: Varies
Reporting: baseline, 6 months

Who is running the clinical trial?

University of California, DavisLead Sponsor
855 Previous Clinical Trials
5,025,308 Total Patients Enrolled

Eligibility Criteria

Age 50 - 85 · All Participants · 2 Total Inclusion Criteria

Mark “Yes” if the following statements are true for you:
References

Frequently Asked Questions

What is the current enrollment tally for participants in this trial?

"Affirmative. According to the clinicaltrials.gov database, this trial is currently searching for suitable participants. This research was initially posted on June 25th 2021 and has been revised as recently as January 31st 2022. The researchers are looking to recruit 15 individuals from one specific site." - Anonymous Online Contributor

Unverified Answer

What are the primary goals of this research initiative?

"The principal objective of this medical trial, tracked across Baseline and 6 months, is to ascertain any fluctuations in mitochondrial function through the production of Adenosine Triphosphate (ATP). Other secondary outcomes being measured include changes in kinetic, postural and rest tremor upper extremity bradykinesia/hypokinesia/dysrhythmia/dyskinesias as quantified by pre-ordained Kinesia One tests; alterations in Fragile X Tremor Ataxia Syndrome (FXTAS) clinical staging via a standardised neurological examination;; plus shifts occurring within subcortical brain" - Anonymous Online Contributor

Unverified Answer

Is the elderly population allowed to partake in this experiment?

"The age range for acceptance into this trial is between 50 and 85 years old." - Anonymous Online Contributor

Unverified Answer

Are there any vacancies available within this research project?

"Affirmative. Clinicaltrials.gov's records demonstrate that this clinical trial is presently recruiting participants, having been first publicized on June 25th 2021 and most recently amended on January 31st 2022. The investigators are seeking 15 patients from one site to take part in the study." - Anonymous Online Contributor

Unverified Answer

May I partake in this research endeavor?

"This research study seeks to recruit 15 individuals with ataxia in the ages of 50-85. All applicants should satisfy two key considerations: A diagnosis of FXTAS and a FMR1 premutation (55 to 200 CGG repeats)." - Anonymous Online Contributor

Unverified Answer
Please Note: These questions and answers are submitted by anonymous patients, and have not been verified by our internal team.