Inhaled Nitric Oxide for Diaphragmatic Hernia

MH
AE
Overseen ByAshley Ebanks
Age: < 18
Sex: Any
Trial Phase: Phase 4
Sponsor: The University of Texas Health Science Center, Houston
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial examines how inhaled nitric oxide (iNO) affects newborns with congenital diaphragmatic hernia (CDH). Researchers aim to determine if stopping iNO during the first days after birth impacts survival rates and the need for additional medical support, such as ECLS (a heart-lung machine). They also assess the cost-effectiveness of using or not using iNO. Eligible participants are babies diagnosed with CDH before one month old and treated at specific centers. As a Phase 4 trial, this research helps clarify how this FDA-approved and effective treatment benefits more patients.

Will I have to stop taking my current medications?

The trial information does not specify whether participants need to stop taking their current medications.

What is the safety track record for Inhaled Nitric Oxide (iNO)?

Research has shown that inhaled nitric oxide (iNO) is generally safe for newborns. However, its effectiveness and safety for specific conditions, such as congenital diaphragmatic hernia (CDH), remain under discussion. Some studies suggest that iNO might not be effective and could even be harmful for babies with CDH.

For example, one study found that iNO might assist babies with CDH who have high blood pressure in their lungs, but it did not provide clear guidance on which babies would benefit most. Another study raised safety concerns, suggesting potential negative effects.

In summary, while iNO is commonly used, opinions vary on its safety and effectiveness for CDH. It is important to consult healthcare providers to understand the potential risks and benefits before participating in a trial involving iNO.12345

Why are researchers enthusiastic about this study treatment?

Researchers are excited about exploring the use of inhaled nitric oxide (iNO) for treating diaphragmatic hernia because it offers a targeted approach to managing pulmonary hypertension, a common complication of the condition. Unlike traditional methods that might involve mechanical ventilation or surgical interventions, iNO is administered directly as a gas that relaxes blood vessels in the lungs, potentially improving oxygenation quickly and effectively. This non-invasive method might reduce the need for more aggressive treatments and improve outcomes in newborns during the critical initial resuscitation period.

What evidence suggests that this trial's treatments could be effective for diaphragmatic hernia?

Research has shown that using inhaled nitric oxide (iNO) for babies with a diaphragmatic hernia yields mixed results. In this trial, one group of participants will receive iNO during their initial resuscitation period, while another group will not. Some studies indicate that many hospitals use iNO, but its effectiveness for these babies remains unclear. Data suggests that iNO does not consistently improve survival rates or reduce the need for additional life support, such as a heart-lung machine (ECLS). Despite its widespread use, evidence suggests that iNO might not always be beneficial and could sometimes even be harmful. This raises questions about its value in treating newborns with this condition.13678

Who Is on the Research Team?

MH

Matthew T. Harting, MD, MS

Principal Investigator

The University of Texas Health Science Center, Houston

Are You a Good Fit for This Trial?

This trial is for newborns with a type of hernia called Bochdalek, diagnosed before they turn one month old. They must be born at or transferred to a participating center within their first week of life. Babies without access to the tested treatment or diagnosed after one month, or those with Morgagni hernia are not eligible.

Inclusion Criteria

Having other medical conditions or abnormalities is allowed for participation.
My Bochdalek hernia is on the right or left side.
I was diagnosed with my condition within the first month of life.
See 2 more

Exclusion Criteria

You do not have access to iNO (inhaled nitric oxide).
Transferred to a CDH Study Group (CDHSG) member center after 1 week of life
I have a hernia in the front part of my diaphragm.
See 1 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Initial Resuscitation and Stabilization

Centers use iNO per their usual protocol during the initial resuscitation period, which includes birth through stabilization and CDH repair

Birth through stabilization and CDH repair

De-implementation

Centers stop using iNO in the initial resuscitation period as part of the de-implementation strategy

Birth through stabilization and CDH repair

Follow-up

Participants are monitored for safety and effectiveness after treatment, including ECLS use and/or mortality until hospital discharge

Up to 12 months from birth

What Are the Treatments Tested in This Trial?

Interventions

  • De-implementation of Inhaled Nitric Oxide (iNO) use
  • Inhaled Nitric Oxide (iNO)
Trial Overview The study aims to see if stopping the use of inhaled Nitric Oxide (iNO) during early care affects survival rates and the need for extracorporeal life support (ECLS). It also looks at whether this change can save healthcare costs without compromising patient outcomes.
How Is the Trial Designed?
2Treatment groups
Active Control
Group I: Inhaled Nitric Oxide (iNO) useActive Control1 Intervention
Group II: De-implementation of Inhaled Nitric Oxide (iNO) useActive Control1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

The University of Texas Health Science Center, Houston

Lead Sponsor

Trials
974
Recruited
361,000+

Citations

Revisiting Inhaled Nitric Oxide Utilization in Congenital ...Nearly half of CDH patients still receive iNO therapy. Given the unclear efficacy of iNO on CDH outcomes, these data represent a call for more prospective ...
2.pubmed.ncbi.nlm.nih.govpubmed.ncbi.nlm.nih.gov/40562092/
A national cohort study of major children's hospitals in the ...Use of iNO in CDH neonates is declining but continues to vary widely among major children's hospitals.
Study Details | NCT05213676 | Inhaled Nitric Oxide (iNO) ...The purpose of this study is to Determine if deimplementation of iNO in the post-natal resuscitation/stabilization phase affects the composite outcome of ECLS ...
4.pubmed.ncbi.nlm.nih.govpubmed.ncbi.nlm.nih.gov/27723858/
Evaluation of Variability in Inhaled Nitric Oxide Use and ...Objective: To describe the spectrum of iNO use among patients with CDH and its association with pulmonary hypertension (pHTN) and mortality.
UTHealth Houston to Lead Data Coordinating Center on ...Previous observational evidence suggests a lack of effectiveness and potential harm from iNO among neonates with CDH, yet it is still widely ...
Initial Oxygenation Response to Inhaled Nitric Oxide Predicts ...Inhaled nitric oxide therapy seems to increase survival in PH due to CDH. No predictive parameters to orient patient selection could be identified.
Evaluation of Variability in Inhaled Nitric Oxide Use and ...This population-based study uses data from the Congenital Diaphragmatic Hernia Study Group registry to assess the association of inhaled ...
Revisiting Inhaled Nitric Oxide Utilization in Congenital ...The primary outcome was in-hospital mortality, and secondary outcomes were extracorporeal membrane oxygenation (ECMO) use, mechanical ventilation duration, ...
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