Enpatoran for Lupus

(Elowen-1 Trial)

CC
Overseen ByCommunication Center
Age: 18+
Sex: Any
Trial Phase: Phase 3
Sponsor: Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany
Pivotal Trial (Near Approval)This treatment is in the last trial phase before FDA approval
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial aims to test the effectiveness and safety of a new treatment called enpatoran for people with lupus, specifically those with skin-related symptoms. Participants will take either the medication or a placebo in tablet form over 24 weeks to assess its impact on reducing these skin issues. The trial is suitable for individuals who have experienced lupus-related skin problems for at least six months. As a Phase 3 trial, this study represents the final step before FDA approval, offering participants an opportunity to contribute to the potential availability of a new treatment for lupus.

Do I have to stop taking my current medications for the trial?

The trial information does not specify if you need to stop taking your current medications. However, stable maintenance therapy with certain medications like mycophenolate, azathioprine, or an oral calcineurin inhibitor is allowed for participants with lupus nephritis.

Is there any evidence suggesting that enpatoran is likely to be safe for humans?

Research has shown that enpatoran was well-tolerated in past studies. In individuals with lupus, the treatment had a manageable safety profile, with no unexpected safety issues or unknown problems. Reports from earlier studies also noted that enpatoran did not present any new safety concerns, which reassures those considering participation in a clinical trial. This suggests that enpatoran is relatively safe for humans based on the available data.12345

Why do researchers think this study treatment might be promising for lupus?

Enpatoran is unique because it targets the TLR7/8 pathway, which plays a key role in the immune system's overactivity associated with lupus. Unlike standard treatments like corticosteroids or hydroxychloroquine, which can have broad effects on the immune system, Enpatoran offers a more targeted approach, potentially reducing side effects. Researchers are excited because this precision could lead to better management of lupus symptoms with fewer complications, offering new hope for patients seeking more tailored therapies.

What evidence suggests that enpatoran might be an effective treatment for lupus?

Research shows that enpatoran, which participants in this trial may receive, might help people with lupus, especially when it affects the skin. In earlier studies, up to 81.5% of patients with severe skin problems experienced a significant reduction in rash severity after using enpatoran. Another study found that 58.6% of patients responded well to the treatment, compared to 31.7% who took a placebo. Enpatoran targets specific parts of the immune system to lower inflammation. It also proved to be well-tolerated, causing few side effects. These encouraging results suggest that enpatoran could help manage lupus symptoms, particularly those related to the skin.24678

Who Is on the Research Team?

MR

Medical Responsible

Principal Investigator

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Are You a Good Fit for This Trial?

This trial is for individuals with active skin symptoms of lupus, with or without systemic disease. They must have a certain severity score, be vaccinated according to local guidelines, and have had lupus for at least 6 months. People with drug-induced lupus, other skin diseases like psoriasis, uncontrolled conditions such as severe asthma or life-threatening lupus complications are excluded.

Inclusion Criteria

Participants with CLASI-A score >= 8 at Screening and Day 1 visits
Other protocol-defined inclusion criteria may apply
I have had skin lupus symptoms for at least 6 weeks.
See 4 more

Exclusion Criteria

Participants with drug-induced lupus (SLE or CLE)
Participants with any condition including dermatological diseases other than cutaneous manifestations of lupus (e.g. psoriasis), any uncontrolled disease (e.g. asthma, chronic obstructive pulmonary disease, interstitial lung disease, bronchiectasis, pulmonary arterial hypertension), or life-threatening manifestations of lupus (e.g. active systemic vasculitis) that in Investigator's or Sponsor/designee's opinion constitutes inappropriate risk or contraindication for participation
I am currently on or recently finished lupus nephritis treatment.
See 4 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive Enpatoran or placebo for 24 weeks

24 weeks
Visits every 4 weeks, with a televisit at Week 2

Follow-up

Participants are monitored for safety and effectiveness after treatment

4-7 weeks

What Are the Treatments Tested in This Trial?

Interventions

  • Enpatoran

Trial Overview

The study tests the efficacy and safety of Enpatoran compared to placebo over 24 weeks in treating cutaneous manifestations of lupus. Participants will visit every four weeks after an initial televisit in week two and take film-coated tablets as part of their treatment.

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Placebo Group

Group I: EnpatoranExperimental Treatment2 Interventions
Group II: PlaceboPlacebo Group2 Interventions

Find a Clinic Near You

Who Is Running the Clinical Trial?

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Lead Sponsor

Trials
60
Recruited
7,900+

Danny Bar-Zohar

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Chief Executive Officer

MD

Danny Bar-Zohar

Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

Chief Medical Officer since 2022

MD

Merck KGaA, Darmstadt, Germany

Industry Sponsor

Trials
449
Recruited
122,000+
Danny Bar-Zohar profile image

Danny Bar-Zohar

Merck KGaA, Darmstadt, Germany

Chief Medical Officer since 2022

MD

Belén Garijo profile image

Belén Garijo

Merck KGaA, Darmstadt, Germany

Chief Executive Officer since 2021

MD

Citations

2025-05-21 Positive Phase 2 Data for Enpatoran

The company announced positive data on enpatoran demonstrating reduction in disease activity in patients with cutaneous lupus erythematosus (CLE) and systemic ...

Enpatoran, a first-in-class, selective, orally administered toll ...

Conclusions Enpatoran was well tolerated and demonstrated favourable safety and PK profiles in patients with SLE and CLE. Although preliminary, ...

Enpatoran Phase 2 Data from Cohort B in SLE

In patients with active skin disease (CLASI-A ≥8), BICLA response rates were up to 58.6% while placebo response rates were 31.7%, and up to 60.5 ...

RANDOMIZED, PLACEBO-CONTROLLED PHASE II ...

At baseline, 59.0% of patients were receiving systemic CS, 38.0% immunosuppressants and 76.0% antimalarials; 71% had moderate-to-severe disease ...

Phase II Trial of Lupus Treatment Enpatoran Shows ...

Among those with severe skin involvement, up to 81.5% of those who received enpatoran had at least 50% improvement in rash severity, and 60.5% ...

2025-06-11 Enpatoran Phase 2 Data from Cohort B in SLE

Enpatoran was well-tolerated and exhibited a manageable safety profile consistent with previous studies, with no new safety signals identified.

7.

pubmed.ncbi.nlm.nih.gov

pubmed.ncbi.nlm.nih.gov/41136221/

Enpatoran, a first-in-class, selective, orally administered toll ...

Conclusions: Enpatoran was well tolerated and demonstrated favourable safety and PK profiles in patients with SLE and CLE. Although preliminary, ...

Merck's Enpatoran to Reduce Disease Activity in CLE and ...

In this cohort, enpatoran was well-tolerated, and exhibited a manageable safety profile consistent with previous studies, with no new safety ...