Brepocitinib for Dermatomyositis

Clinical Trial Site, Haifa, Israel
DermatomyositisBrepocitinib - Drug
Eligibility
18 - 75
All Sexes

Study Summary

This trial is testing a new drug to treat dermatomyositis. The goal is to see if it is better than placebo at reducing symptoms.

Treatment Effectiveness

Phase-Based Effectiveness

2 of 3
Phase 3
This is further along than 85% of similar trials

Study Objectives

1 Primary · 5 Secondary · Reporting Duration: 52 weeks

52 weeks
MMT-8 after 52 weeks of brepocitinib administration QD, in comparison to placebo
Manual Muscle Testing (MMT-8) after 52 weeks of brepocitinib administration QD, in comparison to placebo
TIS responder rate after 52 weeks of brepocitinib administration QD, in comparison to placebo
Time to initiation of rescue medication through 52 weeks of brepocitinib administration QD, in comparison to placebo
Time to use of rescue medication through 52 weeks of brepocitinib administration QD, in comparison to placebo
Total Improvement Score (TIS) at Week 52

Trial Safety

Phase-Based Safety

3 of 3
This is further along than 85% of similar trials

Awards & Highlights

Pivotal Trial
The final step before approval, pivotal trials feature drugs that have already shown basic safety & efficacy.

Trial Design

3 Treatment Groups

Brepocitinib Dose Level 2 PO QD
1 of 3
Brepocitinib Dose Level 1 PO QD
1 of 3
Placebo PO QD
1 of 3

Experimental Treatment

Non-Treatment Group

225 Total Participants · 3 Treatment Groups

Primary Treatment: Brepocitinib · Has Placebo Group · Phase 3

Brepocitinib Dose Level 2 PO QD
Drug
Experimental Group · 1 Intervention: Brepocitinib · Intervention Types: Drug
Brepocitinib Dose Level 1 PO QD
Drug
Experimental Group · 1 Intervention: Brepocitinib · Intervention Types: Drug
Placebo PO QD
Drug
PlaceboComparator Group · 1 Intervention: Placebo · Intervention Types: Drug

Trial Logistics

Trial Timeline

Screening: ~3 weeks
Treatment: Varies
Reporting: 52 weeks

Who is running the clinical trial?

Priovant Therapeutics, Inc.Lead Sponsor
1 Previous Clinical Trials
24 Total Patients Enrolled
Noriko Iikuni, MDStudy DirectorVP, Clinical Development
Christina Crater, MDStudy DirectorSenior Director, Clinical Development

Eligibility Criteria

Age 18 - 75 · All Participants · 2 Total Inclusion Criteria

Mark “Yes” if the following statements are true for you:
You have an ongoing muscle or skin condition during the initial screening.
You have used or are currently using medications such as corticosteroids, hydroxychloroquine or immunosuppressants.

Frequently Asked Questions

Does this research project only consider elderly patients?

"The age limit for this clinical trial is set at 74 years old. All participants must also be of legal age, which is 18 years old in most jurisdictions." - Anonymous Online Contributor

Unverified Answer

How many individuals are taking part in this clinical trial?

"In order for this clinical trial to move forward, we need 225 willing and eligible individuals. The locations where patients can participate in the study include University of Florida Health - Springhill in Gainesville, Florida and University of California - Irvine in Dallas, California." - Anonymous Online Contributor

Unverified Answer

Are there any patients needed for this clinical research at the moment?

"That is correct. As of today, the clinical trial indicated on clinicaltrials.gov is still recruiting patients. The study was originally posted on October 31st, 2020 and was last updated November 4th, 2020. Currently, the goal is to enroll 225 patients from 20 different sites." - Anonymous Online Contributor

Unverified Answer

To whom does this study open enrollment?

"This study is looking for adult patients (18-74 years old) that have been diagnosed with dermatomyositis according to the 2017 EULAR/ACR Classification Criteria. The 225 participants must also exhibit active muscle and skin disease, have prior or current therapy with corticosteroids, hydroxychloroquine, and/or one non-steroid immunosuppressant, weigh more than 40 kg but less than 130 kg, and have a body mass index (BMI) that is below 40 kg/m2." - Anonymous Online Contributor

Unverified Answer

At how many facilities is this research being conducted?

"20 different medical centres are currently recruiting patients for this clinical trial. If you live near any of the following locations - Gainesville, Dallas and Orlando - to name a few, please consider enrolling as it will minimize travel requirements." - Anonymous Online Contributor

Unverified Answer

Could you elaborate on the side effects of Brepocitinib?

"Brepocitinib's safety is rated highly by our team because it has received a score of 3. This number reflects that the drug is currently in Phase 3 testing, meaning that there is both evidence of efficacy and multiple rounds of data supporting safety." - Anonymous Online Contributor

Unverified Answer
Please Note: These questions and answers are submitted by anonymous patients, and have not been verified by our internal team.