BXCL501 for Schizophrenia and Bipolar Disorder

Not currently recruiting at 4 trial locations
MD
Overseen ByMichel Duval, MD
Age: 18+
Sex: Any
Trial Phase: Phase 2
Sponsor: BioXcel Therapeutics Inc
Must be taking: Psychotropic treatment
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests a new treatment, BXCL501, to evaluate its effectiveness for individuals with schizophrenia, bipolar disorder, and similar conditions. The primary focus is on episodes of psychomotor agitation, characterized by restlessness or an inability to sit still. Researchers aim to compare assessments of these episodes by patients, their close contacts, and doctors. Individuals who have experienced an agitation episode requiring treatment in the last 30 days and are on stable medication for their condition might be suitable candidates. As a Phase 2 trial, this research measures the treatment's effectiveness in an initial, smaller group of participants.

Do I need to stop my current medications to join the trial?

You need to be on stable psychotropic treatment for 30 days before the trial and continue it during the study. However, you cannot take certain medications like alpha-1 noradrenergic blockers or alpha-2 adrenergic agonists.

Is there any evidence suggesting that BXCL501 is likely to be safe for humans?

Research has shown that BXCL501, a small film placed under the tongue containing dexmedetomidine, is generally well-tolerated by patients. Earlier studies tested various doses, including 120 micrograms, for safety and effectiveness. Participants handled the treatment well, and it helped manage sudden agitation in people with bipolar disorder and schizophrenia.

Some studies included a large number of patients, providing strong support for these findings. Although mild side effects like drowsiness were reported, the treatment is considered safe for these conditions. The current phase of research indicates that BXCL501 has shown enough promise in earlier studies to warrant continued testing.12345

Why do researchers think this study treatment might be promising for schizophrenia and bipolar disorder?

Unlike the standard treatments for schizophrenia and bipolar disorder, which often involve antipsychotics and mood stabilizers, BXCL501 introduces an innovative approach with its sublingual film delivery of dexmedetomidine. This treatment is unique because it targets the alpha-2 adrenergic receptors, a different mechanism of action compared to traditional options that primarily focus on dopamine and serotonin pathways. The sublingual film allows for rapid absorption and onset of action, potentially offering quicker relief from symptoms. Researchers are excited about BXCL501 because it promises a new pathway for managing these conditions, potentially with fewer side effects and faster results.

What evidence suggests that BXCL501 might be an effective treatment for Schizophrenia and Bipolar Disorder?

Research has shown that BXCL501, a small film placed under the tongue, holds promise for treating restlessness and agitation. In earlier studies, patients felt much calmer just two hours after taking BXCL501 compared to those who took a placebo, which contains no active medicine. This treatment has effectively managed episodes in conditions like bipolar disorder. The FDA recognized its potential by granting it special status for treating agitation related to dementia. These findings suggest that BXCL501 could be a helpful option for managing agitation in schizophrenia and similar disorders. Participants in this trial will receive BXCL501 as a sublingual film to evaluate its effectiveness in these conditions.13567

Who Is on the Research Team?

MM

Matt Mandel, MD

Principal Investigator

BioXcel Therapeutics

Are You a Good Fit for This Trial?

This trial is for individuals with conditions like schizophrenia, bipolar disorder, schizoaffective disorder, and schizophreniform disorder who experience severe restlessness or agitation (psychomotor agitation). Specific eligibility criteria are not provided.

Inclusion Criteria

I've been on stable mental health medication for 30 days and will continue during the study.
Informants must be a spouse, significant other, family member, friend, home health aide, or residence manager of an adult patient who has a clinical diagnosis of bipolar I or bipolar II disorder, schizophrenia, schizoaffective or schizophreniform disorder
Informants must not plan to discontinue contact with the patient during the study period
See 10 more

Exclusion Criteria

Patients who have received an investigational drug within 30 days prior to Baseline
Informants unable to accompany the patient and remain present at the clinical site to complete ratings for the full two-hour data collection period while the patient experiences an acute agitation episode that needs to be treated
I am not pregnant or breastfeeding.
See 10 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

1-2 weeks

Treatment

Participants receive BXCL501 Sublingual film and are assessed for psychomotor agitation measures

2 hours
1 visit (in-person)

Follow-up

Participants are monitored for safety and effectiveness after treatment

1 week

Informant and Patient Training

Assessment of content validity of training materials for informants and patients

Within 7 days of the intervention

What Are the Treatments Tested in This Trial?

Interventions

  • BXCL501
Trial Overview The study tests BXCL501 Sublingual Film's effectiveness in managing psychomotor agitation in patients with certain psychiatric disorders. It aims to compare patient and layperson assessments of treatment outcomes with clinician evaluations.
How Is the Trial Designed?
1Treatment groups
Experimental Treatment
Group I: BXCL501 Sublingual filmExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

BioXcel Therapeutics Inc

Lead Sponsor

Trials
20
Recruited
2,400+

Premier Research Group plc

Industry Sponsor

Trials
65
Recruited
74,200+

John Ratliff

Premier Research Group plc

Chief Executive Officer since 2024

MBA

Dr. Milena Kanova-Petrova

Premier Research Group plc

Chief Medical Officer since 2024

MD

Premier Research Group plc

Collaborator

Premier Research

Collaborator

Citations

Press Release - BioXcel TherapeuticsBXCL501 demonstrated a significant mean reduction in mCGI-S score from baseline compared to placebo at 2 hours across 2,433 treated episodes ...
Press ReleasesBXCL501 has been granted Breakthrough Therapy designation by the FDA for the acute treatment of agitation associated with dementia and Fast ...
Sublingual Dexmedetomidine for Agitation Associated with ...The efficacy and tolerability of 120-µg and 180-µg doses of sublingual dexmedetomidine were evaluated in two similarly designed, randomized, double-blind, ...
Study Supports At-Home Use of Dexmedetomidine ...Notably, an exploratory analysis showed treatment with dexmedetomidine sublingual film was associated with a reduction in symptoms of agitation.
Study Details | NCT04276883 | Dexmedetomidine in the ...This is a definitive study to support the safety and efficacy evaluation of BXCL501 for the acute treatment of agitation in bipolar disorder.
Press ReleaseThe SERENITY At-Home Phase 3 trial is a double-blind, placebo-controlled study designed to evaluate the safety of a 120 mcg dose of BXCL501 for ...
Sublingual Dexmedetomidine for the Treatment of Agitation ...In two phase 3 trials, two dose strengths of sublingual dexmedetomidine 180 mg and 120 mg were safe and effective in managing acute agitation in patients with ...
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