Ropeginterferon Alfa-2b for Chronic Myelomonocytic Leukemia

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Overseen ByVladimir Kustanovich
Age: 18+
Sex: Any
Trial Phase: Phase 2
Sponsor: Jonsson Comprehensive Cancer Center
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests a new treatment called ropeginterferon alfa-2b for individuals with certain blood disorders, including chronic myelomonocytic leukemia (CMML). Ropeginterferon alfa-2b is a long-acting protein that boosts the immune system to combat cancer cells. The trial aims to determine the optimal dose and assess the treatment's safety and effectiveness. Individuals diagnosed with myelodysplastic/myeloproliferative overlap syndromes, who have not previously received similar medications, might be suitable candidates for this trial. As a Phase 2 trial, the research focuses on evaluating the treatment's effectiveness in an initial, smaller group of participants.

Do I need to stop my current medications for this trial?

The trial does not specify if you need to stop all current medications, but you cannot have had other standard or experimental therapies for MDS/MPN within 28 days of starting the study, except for hydroxyurea, which you can continue for up to 28 days after starting the trial.

Is there any evidence suggesting that ropeginterferon alfa-2b is likely to be safe for humans?

Research has shown that ropeginterferon alfa-2b is generally safe. Earlier studies reported no very serious side effects. Some patients experienced moderate side effects, but these were uncommon. People with chronic myelomonocytic leukemia usually tolerate the treatment well. Ropeginterferon alfa-2b is also approved for treating polycythemia vera, another blood condition, indicating it has undergone human safety testing. This approval provides some confidence in its safety for trial participants.12345

Why do researchers think this study treatment might be promising?

Ropeginterferon Alfa-2b is unique because it targets chronic myelomonocytic leukemia (CMML) with a novel mechanism of action using a pegylated interferon. Unlike traditional treatments for CMML, such as hydroxyurea or hypomethylating agents like azacitidine, which focus on reducing leukemic cell proliferation, Ropeginterferon Alfa-2b works by modulating the immune system to fight cancer cells more effectively. Additionally, its administration via subcutaneous injection every two weeks offers a potentially more convenient and manageable treatment schedule. Researchers are excited about its potential to provide a new, effective option with a different approach to managing CMML.

What evidence suggests that ropeginterferon alfa-2b might be an effective treatment for chronic myelomonocytic leukemia?

Research has shown that ropeginterferon alfa-2b can be effective for certain blood cancers. In one study on polycythemia vera, a type of blood cancer, it achieved an important goal in 81% of patients after 12 months, compared to 51% with standard treatment. Ropeginterferon alfa-2b has also managed other blood disorders by controlling blood cell levels and reducing the need for additional treatments. This treatment boosts the immune system and slows cancer cell growth. While these results are promising, more research is needed to fully understand its potential for chronic myelomonocytic leukemia. Participants in this trial will receive ropeginterferon alfa-2b to evaluate its effectiveness specifically for chronic myelomonocytic leukemia.13456

Who Is on the Research Team?

WC

Wanxing Chai-Ho, MD

Principal Investigator

UCLA / Jonsson Comprehensive Cancer Center

Are You a Good Fit for This Trial?

This trial is for adults (18+) with certain blood cancers called myelodysplastic/myeloproliferative neoplasm overlap syndromes or chronic myelomonocytic leukemia. Participants need to have stable organ function, not be pregnant or breastfeeding, and cannot have had prior interferon treatment, recent cancer therapies, severe depression, active infections, or other serious illnesses.

Inclusion Criteria

Platelet count of > 50,000/uL
Absolute neutrophils count (ANC) of > 1000/uL
Serum creatinine =< 2.5 mg/dL
See 7 more

Exclusion Criteria

My spleen is noticeably enlarged on physical exam.
I have been treated with interferon or azacitidine before.
I have had an organ transplant.
See 10 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive ropeginterferon alfa-2b subcutaneously on days 1 and 15 of each 28-day cycle, repeating for up to 24 months

24 months
2 visits per cycle (in-person)

Follow-up

Participants are monitored for safety and effectiveness after treatment completion

24 months
Every 3 months

What Are the Treatments Tested in This Trial?

Interventions

  • Ropeginterferon Alfa-2B

Trial Overview

The study is testing the safety and effectiveness of ropeginterferon alfa-2b—a long-acting immune system protein—given to people with specific blood cancers. The trial includes regular medical tests like bone marrow biopsies and scans to monitor response.

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: Treatment (ropeginterferon alfa-2b)Experimental Treatment6 Interventions

Find a Clinic Near You

Who Is Running the Clinical Trial?

Jonsson Comprehensive Cancer Center

Lead Sponsor

Trials
373
Recruited
35,200+

PharmaEssentia

Industry Sponsor

Trials
24
Recruited
2,800+

Citations

Randomized phase 3 trial of Ropeginterferon alfa-2b ...

The Kaplan-Meier probabilities MRFS by 6, 12, and 24 months after TKI discontinuation were 73% (95%-CI, 62–81%), 64% (53–73%) and 56% (45–66%) ...

Study Details | NCT07468916 | Ropeginterferon Alfa-2b for ...

This phase II trial tests the safety, best dose, and effectiveness of ropeginterferon alfa-2b for the treatment of patients with myelodysplastic ...

Efficacy and safety of ropeginterferon alfa-2b in the treatment ...

In the LOW-PV trial, ropeginterferon alfa-2b achieved the composite endpoint in 81% of patients at 12 months versus 51% with phlebotomy alone, ...

Real-World Evidence on Outcomes and Safety of ...

RopegIFN demonstrated hematological and molecular efficacy across Ph- MPN subtypes and was generally well tolerated. However, its effectiveness appears limited ...

ENDURE: No Added Benefit With Ropeginterferon Alfa-2b ...

Ropeginterferon alfa-2b showed no significant MRFS benefit over observation in CML patients post-TKI cessation. High rates of MMR regain were ...

Long-term efficacy and safety of ropeginterferon alfa-2b under ...

Furthermore, ropeg demonstrated a favorable safety profile, with no Grade 4 or higher adverse events (AEs) observed and grade 3 AEs occurring in ...