An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome
(DAFFODIL™ Trial)
What You Need to Know Before You Apply
What is the purpose of this trial?
This trial is testing a medicine called trofinetide, which is taken by mouth, to see if it is safe for extended use in girls with Rett syndrome. The medicine aims to help the brain work better and reduce the symptoms of the disorder.
Will I have to stop taking my current medications?
The trial information does not specify if you need to stop taking your current medications. However, if you are taking insulin, you must have stopped it at least 12 weeks before the study starts.
Are You a Good Fit for This Trial?
Inclusion Criteria
Timeline for a Trial Participant
Screening
Participants are screened for eligibility to participate in the trial
Treatment
Participants receive oral trofinetide to assess safety and tolerability
Follow-up
Participants are monitored for safety and effectiveness after treatment
What Are the Treatments Tested in This Trial?
Interventions
- Trofinetide
Find a Clinic Near You
Who Is Running the Clinical Trial?
ACADIA Pharmaceuticals Inc.
Lead Sponsor