ANX005 for ALS

No longer recruiting at 18 trial locations
SC
Overseen ByStudy Coordinator
Age: 18+
Sex: Any
Trial Phase: Phase 2
Sponsor: Annexon, Inc.
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial explores a new treatment called ANX005 for people with ALS, a condition affecting nerve cells in the brain and spinal cord. The goal is to determine if ANX005, administered through an IV, can slow the progression of ALS symptoms. Eligible participants should have an ALS diagnosis with weakness starting within the past three years. Participants will receive doses every few weeks for about 22 weeks. Those who frequently visit doctors for ALS and meet these criteria might be suitable for this study. As a Phase 2 trial, this research focuses on measuring the treatment's effectiveness in an initial, smaller group of people.

Will I have to stop taking my current medications?

The trial information does not specify whether you need to stop taking your current medications. It's best to discuss this with the trial coordinators or your doctor.

Is there any evidence suggesting that ANX005 is likely to be safe for humans?

Research has shown that ANX005 has been tested for safety and effectiveness in individuals with conditions such as Guillain-Barré syndrome and ALS. One study found that participants receiving ANX005 were 2.4 times more likely to experience health improvements compared to those who did not receive it, suggesting the treatment's potential promise.

However, ANX005 remains in Phase 2 trials for ALS, meaning detailed safety information is still being gathered. Phase 2 trials typically indicate that the treatment was safe in early studies, but researchers are now examining its effects and any potential side effects in a larger group.

If ANX005 is considered for ALS, it has likely been well-tolerated in earlier studies. Nonetheless, participants must be aware of possible risks and discuss them with their healthcare provider.12345

Why do researchers think this study treatment might be promising for ALS?

Researchers are excited about ANX005 for ALS because it offers a new approach by targeting the complement system, which plays a role in inflammation and nerve damage in ALS. Unlike standard treatments like riluzole and edaravone, ANX005 is designed to prevent the progression of nerve cell damage by inhibiting specific complement proteins. This targeted mechanism could potentially slow down the disease's progression more effectively than current options, bringing hope for improved outcomes in ALS patients.

What evidence suggests that ANX005 might be an effective treatment for ALS?

Research suggests that ANX005, which participants in this trial will receive, may help treat ALS, a disease affecting the nerves. Earlier studies found that ANX005 could slow the disease's progression in patients. It blocks certain proteins that might cause nerve damage in ALS. Although more research is needed, these early results offer hope for its potential to manage ALS symptoms.13678

Who Is on the Research Team?

BH

Benjamin Hoehn, MD, PhD

Principal Investigator

Annexon, Inc.

Are You a Good Fit for This Trial?

This trial is for adults with ALS who have experienced muscle weakness within the last 3 years and have a certain level of lung function. Participants must be vaccinated against specific bacteria or willing to get vaccinated, use effective contraception if of childbearing potential, and not weigh over 150 kilograms.

Inclusion Criteria

If female, must be postmenopausal, surgically sterilized, or agree to use highly effective methods of contraception from Screening through Week 36
You have experienced weakness within the last 3 years before the start of the study.
Your lung function test shows that you can breathe out at least 50% of what is expected based on your age, height, and sex while sitting.
See 5 more

Exclusion Criteria

Clinically significant, ongoing or intercurrent illness, medical condition, or medical history that would jeopardize the safety of the participant, limit participation, or compromise the interpretation of the safety data derived from the participant
You have a high level of antinuclear antibodies in your blood.
You weigh more than 150 kilograms.

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive induction dosing of ANX005 on Days 1 and 5 or 6, followed by maintenance doses every 2 weeks up to Week 22

22 weeks

Follow-up

Participants are monitored for safety and effectiveness after treatment

14 weeks

Long-term follow-up

Participants will be contacted by phone 6 months after study completion

What Are the Treatments Tested in This Trial?

Interventions

  • ANX005
Trial Overview The study tests ANX005 administered through an IV in people with ALS. It's an open-label trial, meaning both researchers and participants know what treatment is being given, conducted across multiple centers.
How Is the Trial Designed?
1Treatment groups
Experimental Treatment
Group I: ANX005Experimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Annexon, Inc.

Lead Sponsor

Trials
14
Recruited
1,500+

Citations

Annexon Reports Significant Progress with its Priority ...ANX005 in Amyotrophic Lateral Sclerosis (ALS): Following encouraging preliminary results which showed slowing of disease progression, full ...
Advancements and challenges in amyotrophic lateral sclerosisStudy of ANX005 in Adults With Amyotrophic Lateral Sclerosis (ALS) ... Efficacy of Multiple Drugs in Amyotrophic Lateral Sclerosis (ALS) ...
Trial: Study of ANX005 in Adults With Amyotrophic Lateral...The study consists of approximately 22 weeks of treatment and approximately 14 weeks of follow-up. All participants will be contacted by phone 6 months after ...
Complement-Targeting Agent ANX005 Demonstrates ...ANX005 at 30 mg/kg significantly improved GBS patient outcomes, achieving primary and secondary endpoints in a phase 3 study. The treatment led ...
A Phase 2a Safety, Tolerability, Pharmacokinetic (PK), and ...Full Study Summary: In this Phase 2a, multi-center, open label, proof-of-biology study, ANX005 will be administered to participants with ALS.
Study of ANX005 in Adults With Amyotrophic Lateral Sclerosis ...This study is a multi-center, open-label study of intravenous (IV) ANX005 in participants with ALS.
ANX005 for ALS · Info for ParticipantsWhat is the purpose of this trial? This trial tests ANX005, an IV medication, in people with ALS to see if it can help manage or slow down their symptoms.
Clinical Trials RegisterPhase 2a Safety, Tolerability, Pharmacokinetic, and Pharmacodynamic Study of Intravenous ANX005 in Subjects with Amyotrophic Lateral Sclerosis.
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