Immunotherapy + Pembrolizumab for Head and Neck Cancer

(BelieveIT-201 Trial)

No longer recruiting at 58 trial locations
MR
JC
EB
EB
AO
Overseen ByAscendis Oncology Clinical Trials
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial
Breakthrough TherapyThis drug has been fast-tracked for approval by the FDA given its high promise

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial explores new treatments for individuals with advanced head and neck cancer that can be surgically removed. Researchers aim to determine if combining experimental drugs (TransCon TLR7/8 Agonist and TransCon IL-2 β/γ) with pembrolizumab, a known cancer drug, is more effective than using pembrolizumab alone. Participants will receive one of these treatments before surgery and will undergo follow-up care after surgery to assess safety and effectiveness. The trial seeks individuals newly diagnosed with Stage III or IVA head and neck cancer that has not spread and who are prepared for surgery. As a Phase 2 trial, this research focuses on evaluating the treatment's effectiveness in an initial, smaller group, offering participants a chance to contribute to the development of potentially more effective therapies.

Do I have to stop taking my current medications for the trial?

The trial protocol does not specify if you need to stop taking your current medications. However, if you are on systemic steroid therapy or other immunosuppressive treatments, you may need to stop them at least 7 days before joining the trial.

Is there any evidence suggesting that this trial's treatments are likely to be safe?

Earlier studies found that the TransCon TLR7/8 Agonist, used alone or with pembrolizumab, was generally well-tolerated, with most patients experiencing no serious side effects. It was also well-tolerated when combined with TransCon IL-2 β/γ in patients who had undergone many previous treatments. These results suggest that the treatment might be safe for participants.

The FDA has approved pembrolizumab for other uses, indicating its safety is well-understood. Based on past research and approvals, the combination of these treatments in the trial is expected to be generally safe. However, participants should stay informed about any new information as the trial continues.12345

Why are researchers excited about this trial's treatments?

Researchers are excited about these treatments for head and neck cancer because they introduce innovative ways to boost the immune system's ability to fight cancer. Unlike traditional treatments like surgery, radiation, or chemotherapy, TransCon IL-2 β/γ and TransCon TLR7/8 Agonist work by enhancing the body’s own immune response. TransCon IL-2 β/γ is designed to activate specific immune cells known as T-cells, while TransCon TLR7/8 Agonist stimulates immune activity directly within the tumor. By combining these agents with pembrolizumab, an established immunotherapy, there’s potential for a more powerful and targeted attack on cancer cells, which could lead to better outcomes for patients.

What evidence suggests that this trial's treatments could be effective for head and neck cancer?

In this trial, participants will receive different treatment combinations. Research has shown that using the TransCon TLR7/8 Agonist with pembrolizumab, one of the combinations being tested, may hold promise for treating cancer. Early results suggest this combination helps the immune system attack cancer cells, and some patients have responded well, which is encouraging.

Another combination in this trial is the TransCon TLR7/8 Agonist combined with TransCon IL-2 β/γ. Studies indicate this combination is generally well-tolerated and can lead to significant improvements. It is designed to enhance the immune system's ability to fight cancer. Both treatments are exciting because they aim to make the immune system work harder against cancer, which could be very effective.12356

Who Is on the Research Team?

JM

Joan Morris

Principal Investigator

Ascendis Pharma Oncology Division A/S

Are You a Good Fit for This Trial?

This trial is for adults with newly diagnosed, resectable Stage III/IVA head and neck squamous cell carcinoma. Participants must have a tumor suitable for surgery, adequate organ function, an ECOG performance status of 0 or 1, and no immunodeficiency or significant cardiac disease. They should not be on high-dose steroids or other immune-suppressing drugs.

Inclusion Criteria

I have a tumor that can be safely injected.
I am scheduled for surgery on my head or neck cancer.
My cancer is a new, operable, non-spreading squamous cell carcinoma.
See 4 more

Exclusion Criteria

Active autoimmune conditions
I have a serious heart condition.
Known bleeding disorder that poses unacceptable risk for bleeding complications from IT injections or biopsies
See 1 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Safety Run-in

Evaluate the safety and tolerability of the two treatment arms: Arm A (TransCon TLR7/8 Agonist plus pembrolizumab) and Arm B (TransCon TLR7/8 Agonist plus TransCon IL-2 β/γ)

6 weeks
2 visits (in-person)

Treatment

Participants receive study drug(s) every 21 days for 2 cycles followed by curative-intent surgery

6 weeks
2 visits (in-person)

Follow-up

Participants are monitored for safety, efficacy, and survival after treatment

Up to 2 years

What Are the Treatments Tested in This Trial?

Interventions

  • Pembrolizumab
  • TransCon IL-2 β/γ
  • TransCon TLR7/8 Agonist
Trial Overview The trial tests the safety and effectiveness of two experimental treatments (TransCon TLR7/8 Agonist with pembrolizumab in Arm A; TransCon TLR7/8 Agonist with TransCon IL-2 β/γ in Arm B) against pembrolizumab alone (Arm C). It includes a safety run-in phase followed by randomized comparison over up to two years post-surgery.
How Is the Trial Designed?
3Treatment groups
Experimental Treatment
Active Control
Group I: TransCon TLR7/8 Agonist in combination with pembrolizumabExperimental Treatment2 Interventions
Group II: TransCon TLR7/8 Agonist in combination with TransCon IL-2 β/γExperimental Treatment2 Interventions
Group III: PembrolizumabActive Control1 Intervention

Pembrolizumab is already approved in United States, European Union, United Kingdom for the following indications:

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Approved in United States as KEYTRUDA for:
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Approved in European Union as KEYTRUDA for:
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Approved in United Kingdom as KEYTRUDA for:

Find a Clinic Near You

Who Is Running the Clinical Trial?

Ascendis Pharma A/S

Lead Sponsor

Trials
15
Recruited
1,600+

Ascendis Pharma Oncology Division A/S

Lead Sponsor

Trials
3
Recruited
560+

Citations

NCT05980598 | TransCon (TC) TLR7/8 Agonist, TC IL-2 β/ ...The purpose of this trial is to evaluate the safety and efficacy of TransCon TLR7/8 Agonist, TransCon IL-2 β/γ, and pembrolizumab given prior to curative ...
TransCon IL-2 β/γ alone or in combination with ...Conclusions: TC-IL2 β/γ alone and in combination with P or TransCon TLR7/8 Agonist is generally well-tolerated with meaningful clinical ...
TransCon (TC) TLR7/​8 Agonist, TC IL-2 β/​γ ...About this study. The purpose of this trial is to evaluate the safety and efficacy of TransCon TLR7/8 Agonist, TransCon IL-2 β/γ, ...
NCT04799054 | A Study of TransCon TLR7/8 Agonist With ...This Phase 1/2 study will evaluate TransCon TLR7/8 Agonist as monotherapy or in combination with pembrolizumab in dose escalation and dose expansion.
Study of TransCon TLR7/8 Agonist, TransCon IL-2 β/γ, and ...This study investigates the efficacy of TransCon TLR7/8 Agonist, TransCon IL-2 β/γ, and Pembrolizumab in treating patients with Stage III-IVA Resectable ...
NCT04799054 | A Study of TransCon TLR7/8 Agonist With ...This Phase 1/2 study will evaluate TransCon TLR7/8 Agonist as monotherapy or in combination with pembrolizumab in dose escalation and dose expansion.
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