Ruxolitinib + Azacitidine for Acute Myeloid Leukemia

Age: 18+
Sex: Any
Trial Phase: Phase 1
Sponsor: OHSU Knight Cancer Institute
Must be taking: Ruxolitinib
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This phase I trial studies the side effects and best dose of ruxolitinib (Rux) therapy alone (monotherapy) followed by Rux plus azacitidine (AZA) maintenance therapy and to see how well it works in treating patients with acute myeloid leukemia (AML) who are undergoing reduced intensity allogeneic hematopoietic stem cell transplantation (alloHSCT). AlloHSCT provides the only chance for cure for many patients with AML. AlloHSCT is a procedure in which a person receives blood-forming stem cells (cells from which all blood cells develop) from a genetically similar, but not identical, donor. This is often a sister or brother, but could be an unrelated donor. One of the common reasons for death after an alloHSCT is graft versus host disease (GVHD), which occurs when the transplanted cells from the donor attacks the recipient's normal cells. Ruxolitinib is in a class of medications called kinase inhibitors. It works to treat GVHD by blocking the signals of the cells that cause GVHD. Azacitidine is in a class of medications called demethylation agents. It works by helping the bone marrow to produce normal blood cells and by killing abnormal cells in the bone marrow. Giving Rux after the transplant may stop GVHD from occurring. Maintenance therapy with AZA, may help prevent or delay cancer from coming back. Giving Rux monotherapy followed by Rux plus AZA maintenance therapy may be safe, tolerable, and/or effective in treating patients with AML who are undergoing alloHSCT.

Who Is on the Research Team?

JN

Jennifer N Saultz

Principal Investigator

OHSU Knight Cancer Institute

Are You a Good Fit for This Trial?

Inclusion Criteria

I am 18 years old or older.
I have received fludarabine or melphalan treatment.
I am willing to sign a consent form before starting the study.
See 7 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

4 weeks
1 visit (in-person)

Treatment Part A

Patients undergo reduced intensity conditioning followed by alloHSCT and receive ruxolitinib monotherapy

35 days
Multiple visits (in-person)

Treatment Part B

Patients receive ruxolitinib and azacitidine maintenance therapy

8 cycles of 28 days each
Monthly visits (in-person)

Follow-up

Participants are monitored for safety and effectiveness after treatment

Up to 2 years
Regular visits as per institutional practice

What Are the Treatments Tested in This Trial?

Interventions

  • Azacitidine
  • Ruxolitinib

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: Treatment (ruxolitinib, azacitidine)Experimental Treatment14 Interventions

Find a Clinic Near You

Who Is Running the Clinical Trial?

OHSU Knight Cancer Institute

Lead Sponsor

Trials
239
Recruited
2,089,000+

Incyte Corporation

Industry Sponsor

Trials
408
Recruited
66,800+
Steven Stein profile image

Steven Stein

Incyte Corporation

Chief Medical Officer since 2015

MD from University of Witwatersrand

Hervé Hoppenot profile image

Hervé Hoppenot

Incyte Corporation

Chief Executive Officer since 2014

MBA from ESSEC Business School

Oregon Health and Science University

Collaborator

Trials
1,024
Recruited
7,420,000+