20 Participants NeededMy employer runs this trial

HABIT-ILE + FST for Spinal Muscular Atrophy

AM
AC
Overseen ByAstrid Carton de Tournai, PhD
Age: < 18
Sex: Any
Trial Phase: Academic
Sponsor: Teachers College, Columbia University
Must be taking: Disease-modifying therapies
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This single-arm pilot study will assess the preliminary effectiveness of an intensive motor skill intervention (HABIT-ILE) combined with functional strength training (FST) in children with SMA who are receiving disease-modifying therapies. Participants will attend a HABIT-ILE + FST summer camp for 6 hours per day over a 3-week period, totaling 90 hours of training.

Are You a Good Fit for This Trial?

Inclusion Criteria

I have been diagnosed with spinal muscular atrophy (SMA).
I am between 5 and 17 years old.
* Complete all pre- and post-intervention assessments
See 4 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants attend a HABIT-ILE + FST summer camp for 6 hours per day over a 3-week period, totaling 90 hours of training

3 weeks
Daily visits (in-person)

Follow-up

Participants are monitored for safety and effectiveness after treatment, with assessments at baseline, immediately after the intervention, and 3 months follow-up

3 months

What Are the Treatments Tested in This Trial?

Interventions

  • Combined Hand-Arm Bimanual Intensive Therapy Including Lower Extremities (HABIT-ILE) + functional strength training (FST)

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: HABIT-ILE + FSTExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Teachers College, Columbia University

Lead Sponsor

Trials
27
Recruited
6,100+