400 Participants Needed

Sutimlimab for Cold Agglutinin Disease

(CADENCE Trial)

Recruiting at 89 trial locations
TT
IA
BM
Overseen ByBeatrice Martin
Age: 18+
Sex: Any
Trial Phase: Academic
Sponsor: Recordati Rare Diseases
Must be taking: Sutimlimab
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial gathers real-world information about individuals with cold agglutinin disease (CAD) or cold agglutinin syndrome (CAS). It aims to understand how these conditions affect daily life and includes a group of CAD patients treated with sutimlimab, a medication designed to manage CAD symptoms. The trial focuses on those who have previously participated in other sutimlimab studies. Individuals with CAD or CAS who are not currently in another trial may be suitable candidates. As a Phase 4 trial, this research helps to understand how the FDA-approved treatment benefits more patients, offering valuable insights for those considering participation.

Do I have to stop taking my current medications for this trial?

The trial information does not specify whether you need to stop taking your current medications. It's best to discuss this with the trial coordinators or your doctor.

What is the safety track record for sutimlimab?

Research shows that sutimlimab is generally safe for people with cold agglutinin disease (CAD). Studies found that patients taking sutimlimab experienced few serious side effects. The most common issues were mild, such as headaches and infections, and were not serious for most people.

Additionally, long-term studies indicate that sutimlimab remains safe and effective over time. Participants reported a better quality of life, suggesting that the benefits outweigh any minor side effects.

Overall, evidence suggests that sutimlimab is a safe option for treating CAD, based on previous research.12345

Why are researchers excited about this trial?

Sutimlimab is unique because it targets the underlying cause of cold agglutinin disease (CAD) by inhibiting the C1s protein in the complement pathway, which is different from standard treatments like corticosteroids or rituximab that mainly manage symptoms. This targeted mechanism can potentially reduce hemolysis, or the destruction of red blood cells, more effectively and with fewer side effects. Researchers are excited about sutimlimab because it offers a more precise approach, potentially improving the quality of life for patients with CAD by directly addressing the disease process.

What is the effectiveness track record for sutimlimab in treating cold agglutinin disease?

Research has shown that sutimlimab effectively treats cold agglutinin disease (CAD). In this trial, participants with CAD will receive sutimlimab. Studies have found that it reduces the breakdown of red blood cells, anemia, and fatigue, leading to fewer blood transfusions. Reports indicate that sutimlimab also improves patients' overall quality of life. These findings suggest that sutimlimab can help manage symptoms and enhance daily life for those with CAD.24678

Who Is on the Research Team?

IA

Ignacio Alvarez Rojo

Principal Investigator

RECORDATI GROUP

Are You a Good Fit for This Trial?

Inclusion Criteria

Patient able to understand the purpose of the study and who (or whose legally authorized representative) provided signed and dated informed consent and authorization to use protected health information in accordance with national and local subject privacy regulations
Patient with a diagnosis of CAD or CAS as per Investigator judgment based on the diagnosis criteria listed in study protocol

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Enrollment

Participants with CAD or CAS are enrolled in the registry to collect data on disease characteristics and treatment patterns

Up to 6 years

Follow-up

Participants are monitored for disease characteristics, treatment patterns, and health-resource utilization

Up to 6 years

What Are the Treatments Tested in This Trial?

Interventions

  • Sutimlimab

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Group I: cold agglutinin syndrome (CAS)Experimental Treatment0 Interventions
Group II: cold agglutinin disease (CAD)Experimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Recordati Rare Diseases

Lead Sponsor

Trials
14
Recruited
540+

RECORDATI GROUP

Lead Sponsor

Trials
13
Recruited
4,500+

Sanofi

Lead Sponsor

Trials
2,246
Recruited
4,085,000+
Paul Hudson profile image

Paul Hudson

Sanofi

Chief Executive Officer since 2019

Degree in Economics from Manchester Metropolitan University

Christopher Corsico profile image

Christopher Corsico

Sanofi

Chief Medical Officer

MD from Cornell University, MPH in Chronic Disease Epidemiology from Yale University

Citations

1.

pubmed.ncbi.nlm.nih.gov

pubmed.ncbi.nlm.nih.gov/38733355/

Cost-effectiveness of sutimlimab in cold agglutinin disease

Exploratory threshold analyses showed that significant price reduction (>80%) or time-limited treatment (<18 months) followed by lifelong ...

CADENZA study Part B - eClinicalMedicine

The CADENZA Part B results support the sustained efficacy and safety of sutimlimab for treatment of CAD; however, upon discontinuation disease ...

Sutimlimab in patients with cold agglutinin disease: results of ...

Sutimlimab reduced hemolysis, anemia, and fatigue in patients with CAD without transfusion requirement. Sutimlimab treatment was generally well ...

Long-term sutimlimab improves quality of life for patients ...

Sutimlimab improves quality of life in patients with cold agglutinin disease: results of patient-reported outcomes from the CARDINAL study.

Cost‐effectiveness of sutimlimab in cold agglutinin disease

Sutimlimab in patients with cold agglutinin disease: results of the randomized placebo-controlled phase 3 CADENZA trial. Blood. 2022; 140(9): ...

Combined Safety Data for Sutimlimab in Cold Agglutinin ...

Combined Safety Data for Sutimlimab in Cold Agglutinin Disease: A Post-Hoc Analysis of the Phase 3 Cardinal and Cadenza Studies Available.

Long-term safety profile of sutimlimab in adult Japanese ...

The results of global phase 3 clinical trials, CARDINAL and CADENZA, have demonstrated robust data that sutimlimab is effective and well ...

Sutimlimab in Cold Agglutinin Disease

We conducted a 26-week multicenter, open-label, single-group study to assess the efficacy and safety of intravenous sutimlimab in patients with cold agglutinin ...