NT-501 Implant for Macular Telangiectasia

Not currently recruiting at 2 trial locations
EZ
PD
Overseen ByPatty Davis
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Pivotal Trial (Near Approval)This treatment is in the last trial phase before FDA approval
Prior Safety DataThis treatment has passed at least one previous human trial
Approved in 1 JurisdictionThis treatment is already approved in other countries

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests a new implant called NT-501, an encapsulated cell therapy, to determine its effectiveness for macular telangiectasia type 2, a condition affecting vision. The trial aims to assess the implant's efficacy and safety. Suitable participants have been diagnosed with MacTel and experience vision issues such as blurry vision or difficulty reading. The implant is placed in one eye to evaluate its potential to improve vision. Participants should not have received certain other eye treatments recently. As a Phase 3 trial, this study represents the final step before FDA approval, offering participants the opportunity to contribute to a potentially groundbreaking treatment for vision improvement.

Do I need to stop my current medications for the trial?

The trial does not specify if you need to stop taking your current medications. However, if you have a chronic requirement for ocular medications, you may be excluded unless it's for artificial tears or one glaucoma medication for early or intermediate primary open-angle glaucoma.

What prior data suggests that the NT-501 implant is safe for treating macular telangiectasia?

Research has shown that the NT-501 CNTF implant is safe and well-tolerated in earlier studies. For instance, in studies involving individuals with macular telangiectasia (a rare eye disease), the NT-501 implant reduced vision loss compared to placebo procedures, demonstrating promise without major side effects. Another study found it safe for patients with primary open-angle glaucoma (a common type of glaucoma), with no significant safety concerns reported.

These findings suggest that the NT-501 implant is generally well-tolerated. As this is a Phase 3 trial, the treatment has already undergone testing for safety and effectiveness, but it is still being studied to confirm its efficacy in a larger group. Prospective participants should find these results encouraging, but discussing any concerns with the study team is advisable.12345

Why do researchers think this study treatment might be promising for macular telangiectasia?

Unlike the standard treatments for Macular Telangiectasia, which often include eye injections or laser therapy, the NT-501 implant offers a unique approach. This implant continuously releases ciliary neurotrophic factor (CNTF) directly into the eye, providing long-term treatment without the need for frequent doctor visits. Researchers are excited because this delivery method could potentially offer sustained benefits and protect the retina over time, which might result in better vision preservation for patients.

What evidence suggests that the NT-501 implant is effective for macular telangiectasia?

Studies have shown that the NT-501 implant effectively treats macular telangiectasia type 2. Research indicates that it can slow retinal damage and significantly reduce the loss of certain eye parts compared to no treatment. Specifically, previous patients demonstrated both structural and functional improvements in their eyes after receiving the implant. The treatment is considered safe and well-tolerated, with promising results in maintaining eye health. This therapy delivers a substance called ciliary neurotrophic factor, which helps protect nerve cells in the eye. Participants in this trial will receive the NT-501 CNTF implant in one eye using the Medica Hollow Fiber Membrane (MHFM).12467

Who Is on the Research Team?

TA

Thomas Aaberg, Jr., MD

Principal Investigator

Neurotech Pharmaceuticals

Are You a Good Fit for This Trial?

This trial is for individuals with a condition affecting the blood vessels in their eyes, known as macular telangiectasia type 2. Specific eligibility details are not provided, but typically participants must meet certain health standards and may be required to have a particular stage or severity of the condition.

Inclusion Criteria

I can focus steadily and have clear enough vision for quality retinal images.
Subject must have a break in the ellipsoid zone (EZ) (area of IS/OS loss) as measured by SD-OCT between 0.16 and 2.00 millimeters squared.
Subject or their legally authorized representative must be able to provide written informed consent to participate in the study, in accordance with the International Conference on Harmonisation Good Clinical Practices guidelines, and local regulations, before initiating any study-related procedures.
See 3 more

Exclusion Criteria

I have been diagnosed with a specific eye condition affecting my retina.
I am currently undergoing chemotherapy.
Subject with a history of ocular herpes virus in either eye.
See 17 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive the NT-501 CNTF implant in one eye using the Medica Hollow Fiber Membrane (MHFM)

12 months
Regular visits as per study protocol

Follow-up

Participants are monitored for safety and effectiveness after treatment

4 weeks

What Are the Treatments Tested in This Trial?

Interventions

  • NT-501
Trial Overview The study is testing NT-501 implants which release CNTF (a protein that could help eye cells) using MHFM technology. It aims to see if this can safely improve vision or slow vision loss over time in those with macular telangiectasia type 2.
How Is the Trial Designed?
1Treatment groups
Experimental Treatment
Group I: NT-501 CNTF Implant with Medica Hollow Fiber Membrane (MHFM)Experimental Treatment1 Intervention

NT-501 is already approved in United States for the following indications:

🇺🇸
Approved in United States as NT-501 for:

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Who Is Running the Clinical Trial?

Neurotech Pharmaceuticals

Lead Sponsor

Trials
12
Recruited
680+

Citations

1.pubmed.ncbi.nlm.nih.govpubmed.ncbi.nlm.nih.gov/40693847/
Cell-Based Ciliary Neurotrophic Factor Therapy for ...NT-501 for MacTel resulted in statistically significantly reduced EZA loss compared with sham procedures.
NCT03316300 | A Study to Determine the Safety and ...This study is a phase 3, randomized, multi-center study to evaluate the efficacy and safety of the NT-501 implants in participants with macular telangiectasia ...
Phase I NT-501 Ciliary Neurotrophic Factor Implant Trial for ...The NT-501 CNTF implant was safe and well tolerated in eyes with POAG. Eyes with the implant demonstrated both structural and functional improvements.
Cell-Based Ciliary Neurotrophic Factor Therapy for Macular ...Revakinagene taroretcel (NT-501) is an encapsulated cell therapy producing ciliary neurotrophic factor that slowed retinal degeneration in ...
Neuroprotectant Treatment for MacTel Type 2Using NT-501 encapsulated cell therapy (revakinagene taroretcel) is safe and effective for treating macular telangiectasia (MacTel) type 2, suggest the results ...
Phase I NT-501 Ciliary Neurotrophic Factor Implant Trial for ...The NT-501 CNTF implant was safe and well tolerated in eyes with POAG. Eyes with the implant demonstrated both structural and functional ...
A Phase 2 Multicenter Randomized Clinical Trial of Ciliary ...A Phase I trial designed to assess the safety of the CNTF procedures by the NT-501 implant in patients with MacTel type 2 has completed enrollment (N=7) and ...
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