MT-125 for Glioblastoma

(NOVA-GBM Trial)

Not yet recruiting at 2 trial locations
Age: 18+
Sex: Any
Trial Phase: Phase 1 & 2
Sponsor: Myosin Therapeutics Inc.
Must be taking: Steroids
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This is a Phase 1, single-arm MT-125 dose escalation study followed by a Phase 2, randomized parallel design dose expansion phase, to determine the safety and tolerability of MT-125 administered 5 consecutive days a week with 2 days off for the 6 weeks of outpatient treatment of Radiotherapy (RT) plus TMZ. Participants with newly diagnosed histologically or molecularly confirmed IDH wild type and MGMT methylated GBM will be eligible to enroll. The dose-limiting toxicity (DLT) observation window will be 6 weeks, starting with the first dose of MT-125 administration and chemoradiation. A Bayesian Optimal Interval (BOIN) adaptive trial design will be used to efficiently evaluate up to four dose levels. Secondary endpoints for this Phase 1/2 study will include determination of the MTD, the systemic PK of MT-125, and the RP2D of MT-125. Once the MTD is defined, additional participants will be enrolled as part of an expansion cohort, with a randomized parallel design, which will include up to 2 dose levels which are expected to be MTD and one dose below the MTD. Up to 36 participants will be enrolled in the study (up to 24 participants in the dose escalation phase and up to a total of 12 participants maximum per dose level for the two expansion cohorts).

Are You a Good Fit for This Trial?

This trial is for adults (18+) with newly diagnosed glioblastoma that is IDH wildtype and MGMT methylated. Participants must be in reasonably good physical condition, have adequate blood counts, liver and kidney function, and stable clotting tests.

Inclusion Criteria

7. Serum eGFR ≥60 ml/min
I am 18 years old or older.
2. Absolute neutrophil count (ANC) ≥1500/mm3
See 7 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive MT-125 with chemoradiation for 6 weeks, administered 5 consecutive days a week with 2 days off

6 weeks
Weekly visits for treatment administration

Dose Escalation

Evaluation of up to four dose levels using a Bayesian Optimal Interval (BOIN) design to determine the maximum tolerated dose (MTD)

6 weeks

Randomized Expansion

Participants are enrolled into a randomized, parallel dose expansion cohort to receive either MTD or one dose lower than MTD

6 weeks

Follow-up

Participants are monitored for safety and effectiveness after treatment, including overall response rate (ORR), progression-free survival (PFS6), and overall survival (OS)

Up to 1 year

What Are the Treatments Tested in This Trial?

Interventions

  • MT-125

Trial Overview

The study is testing different doses of a new drug called MT-125 given along with standard chemoradiation (radiotherapy plus temozolomide) to see if it’s safe and tolerable. The trial has two phases: first finding the best dose, then comparing selected doses.

How Is the Trial Designed?

5

Treatment groups

Experimental Treatment

Group I: MT-125 at MTD and one dose lower than MTDExperimental Treatment1 Intervention
Group II: MT-125 at 83.5 mgExperimental Treatment1 Intervention
Group III: MT-125 at 50 mgExperimental Treatment1 Intervention
Group IV: MT-125 at 25 mgExperimental Treatment1 Intervention
Group V: MT-125 at 100 mgExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Myosin Therapeutics Inc.

Lead Sponsor

Mayo Clinic

Collaborator

Trials
3,427
Recruited
3,221,000+