32 Participants NeededMy employer runs this trial

Efimosfermin Alfa for Non-alcoholic Fatty Liver Disease

Recruiting at 2 trial locations
Age: 18+
Sex: Any
Trial Phase: Phase 1
Sponsor: GlaxoSmithKline
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This clinical trial tests a new treatment called efimosfermin alfa for individuals with non-alcoholic fatty liver disease, specifically targeting those with liver damage (hepatic impairment). The study aims to understand how the body processes the drug and its safety for individuals with moderate to severe liver issues, regardless of alcohol consumption. Participants should have stable chronic liver problems due to fat buildup in the liver, with or without alcohol use, and face daily challenges from their liver condition. As a Phase 1 trial, this research focuses on understanding how the treatment works in people, offering participants the opportunity to be among the first to receive this new treatment.

Is there any evidence suggesting that efimosfermin alfa is likely to be safe for humans?

Research has shown that efimosfermin alfa is generally safe for people with liver conditions. In earlier studies, most participants tolerated it well. These studies found that efimosfermin alfa could reduce liver fat and improve liver health over time. However, like any treatment, it may cause side effects. Some participants experienced mild issues such as headaches or fatigue, while serious side effects were rare. This safety record makes efimosfermin alfa a promising option for those considering participation in a clinical trial for liver disease treatments.12345

Why do researchers think this study treatment might be promising for fatty liver disease?

Most treatments for non-alcoholic fatty liver disease (NAFLD) focus on lifestyle changes, like diet and exercise, or managing conditions like diabetes and high cholesterol with medications. But Efimosfermin Alfa works differently, targeting Metabolic Dysfunction-Associated Steatohepatitis (MASH) directly. Researchers are excited because it offers a new approach by addressing liver inflammation and damage, regardless of alcohol use, and could potentially benefit patients with varying levels of liver impairment. This could make a big difference for people who haven’t found success with existing treatments.

What evidence suggests that efimosfermin alfa might be an effective treatment for non-alcoholic fatty liver disease?

Research shows that efimosfermin alfa, a treatment for liver disease, has promising results. Studies have found that it can greatly reduce liver fat and improve liver function in people with metabolic liver conditions. In this trial, all participants will receive efimosfermin alfa, grouped by the severity of their hepatic impairment and alcohol consumption. In clinical trials, participants experienced a decrease in signs of liver damage and scarring. Efimosfermin alfa is also generally well tolerated. These findings suggest that efimosfermin alfa may help people with liver disease improve their health.25678

Who Is on the Research Team?

GC

GSK Clinical Trials

Principal Investigator

GlaxoSmithKline

Are You a Good Fit for This Trial?

Inclusion Criteria

I am male or female.
I have stable, moderate to severe liver cirrhosis (Child-Pugh B or C) for over 6 months.
Body Mass Index (BMI) within the range 23 - 40 kilogram per square meter (kg/m^2)
See 1 more

Exclusion Criteria

Participants with transjugular intrahepatic portosystemic shunt (TIPS) placement
History or presence of drug abuse
I have had a liver transplant or am currently waiting for one.
See 23 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Participants receive a single dose of efimosfermin alfa to evaluate pharmacokinetics and safety

1 day
1 visit (in-person)

Follow-up

Participants are monitored for safety and effectiveness after receiving the single dose

4 weeks

What Are the Treatments Tested in This Trial?

Interventions

  • Efimosfermin Alfa

How Is the Trial Designed?

3

Treatment groups

Experimental Treatment

Group I: Efimosfermin alfa in severe hepatic impairment participants due to MASH regardless of alcohol useExperimental Treatment1 Intervention
Group II: Efimosfermin alfa in participants with moderate hepatic impairment due to MASH without alcoholExperimental Treatment1 Intervention
Group III: Efimosfermin alfa in participants with moderate hepatic impairment due to MASH with alcoholExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

GlaxoSmithKline

Lead Sponsor

Trials
4,834
Recruited
8,389,000+
Headquarters
London, UK
Known For
Vaccines & Medicines
Top Products
**Advair (salmeterol, fluticasone propionate)**, **Shingrix (shingles vaccine)**, **Augmentin (amoxicillin/clavulanate potassium)**, **Ventolin (salbutamol sulfate)
Dame Emma Walmsley profile image

Dame Emma Walmsley

GlaxoSmithKline

Chief Executive Officer since 2017

MA in Classics and Modern Languages from Oxford University

Dr. Hal Barron profile image

Dr. Hal Barron

GlaxoSmithKline

Chief Medical Officer since 2018

MD from Harvard Medical School

Citations

1.

pubmed.ncbi.nlm.nih.gov

pubmed.ncbi.nlm.nih.gov/41655584/

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