63 Participants NeededMy employer runs this trial

Anumigilimab for Sickle Cell Disease

Recruiting at 2 trial locations
Age: 18+
Sex: Any
Trial Phase: Phase 2
Sponsor: CSL Behring
Must be taking: Hydroxyurea
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests a new treatment called anumigilimab for individuals with sickle cell disease. The main goal is to determine if anumigilimab is safe when administered under the skin at the highest tolerable dose. Participants will have their dose increased over 12 weeks, followed by a continuation at this dose for another 52 weeks. Eligible participants must have a confirmed diagnosis of sickle cell disease and have experienced 1 to 12 pain crises requiring medical treatment in the past year. As a Phase 2 trial, this research focuses on assessing the treatment's effectiveness in an initial, smaller group of people.

Is there any evidence suggesting that anumigilimab is likely to be safe for humans?

A previous study tested anumigilimab in adults with sickle cell disease (SCD) to assess its safety. This research remains in an early stage, so scientists are still determining the treatment's safety and tolerability. The study aims to identify the highest dose that people can take without serious side effects. For those considering joining a trial, this information highlights that safety is a top priority, though more research is needed to fully understand the risks.12345

Why do researchers think this study treatment might be promising for sickle cell disease?

Anumigilimab is unique because it offers a novel approach to managing Sickle Cell Disease (SCD) by targeting the underlying inflammation that contributes to the disease's complications. Unlike current standard treatments, like hydroxyurea or blood transfusions, which focus on reducing sickle cell formation or managing symptoms, Anumigilimab acts by modulating the immune response, potentially reducing pain crises and organ damage. Researchers are particularly excited about this treatment because it represents a targeted therapy with the potential for fewer side effects and improved quality of life for patients with SCD.

What evidence suggests that anumigilimab might be an effective treatment for sickle cell disease?

Research has shown that anumigilimab, which participants in this trial may receive, blocks signals that cause inflammation and pain in sickle cell disease (SCD). In animal studies, this treatment reduced harmful cell activities. It specifically targets neutrophils, cells that can cause inflammation and damage in SCD. By reducing these harmful effects, anumigilimab may help manage pain and other symptoms of the disease. Although research in humans is ongoing, its mechanism suggests potential benefits for people with SCD.12467

Who Is on the Research Team?

SD

Study Director

Principal Investigator

CSL Behring

Are You a Good Fit for This Trial?

Inclusion Criteria

I've had 1 to 12 severe pain crises treated at a hospital with strong painkillers in the last year.
I am 18 years old or older.
I have been on a stable dose of Hydroxyurea for at least 30 days.
See 2 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Dose Escalation

Participants receive anumigilimab with dose escalation to determine individual maximum tolerated dose (MTD)

12 weeks

Maintenance

Participants receive anumigilimab at the determined MTD

52 weeks

Follow-up

Participants are monitored for safety and effectiveness after treatment

11 weeks

What Are the Treatments Tested in This Trial?

Interventions

  • Anumigilimab

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Placebo Group

Group I: AnumigilimabExperimental Treatment1 Intervention
Group II: PlaceboPlacebo Group1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

CSL Behring

Lead Sponsor

Trials
204
Recruited
1,207,000+
Dr. Paul McKenzie profile image

Dr. Paul McKenzie

CSL Behring

Chief Executive Officer since 2023

PhD in Chemical Engineering from Carnegie Mellon University, B.S. in Chemical Engineering from the University of Pennsylvania

Dr. Bill Mezzanotte profile image

Dr. Bill Mezzanotte

CSL Behring

Chief Medical Officer since 2021

MD from Duke University

Citations

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell ...

The DMC can recommend to the sponsor that the trial be stopped if it is not effective, is harming participants, or is unlikely to serve its scientific purpose.

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell ...

This is a phase 2a, global, multicenter, randomized, double-blind, placebo-controlled study investigating the safety of anumigilimab ...

Anumigilimab by CSL for Sickle Cell Disease: Likelihood of ...

Anumigilimab is under clinical development by CSL and currently in Phase I for Sickle Cell Disease. According to GlobalData, Phase I drugs for Sickle Cell ...

Recent Advances in Sickle-Cell Disease Therapies - PMC - NIH

The objective of this article is to evaluate post-approval studies of crizanlizumab, voxelotor, and L-glutamine in SCD, with a focus on real-world efficacy, ...

anumigilimab (CSL324) / CSL Behring

... sickle cell disease: Target for a new phase 2 trial (ASH 2025) - "CSL324 was safe and welltolerated in repeat-dose toxicological studies in non-human ...

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell ...

The primary aim of the study is to assess the safety of anumigilimab in participants with SCD. Participants will be treated for 64 weeks: for 12 ...

A study to assess the safety of Anumigilimab in adults ...

This study focuses on individuals living with Sickle Cell Disease, a condition that affects red blood cells, causing them to become misshapen like a ...