46 Participants NeededMy employer runs this trial

ALN-SNCA for Parkinson's Disease

Recruiting at 1 trial location
CT
Overseen ByClinical Trials Administrator
Age: 18+
Sex: Any
Trial Phase: Phase 1
Sponsor: Regeneron Pharmaceuticals

What You Need to Know Before You Apply

What is the purpose of this trial?

This study is researching an experimental drug called ALN-SNCA (called "study drug"). The study is focused on people with early Parkinson's disease, a disorder of the nervous system that affects movement. Parkinson's disease is caused by a gradual loss of nerve cells in the brain, especially those due to the harmful build-up of a protein called α-synuclein.

The aim of the study is to see if the study drug is safe and tolerated well enough to continue testing it in future studies and what side effects may happen from taking the study drug.

The study is looking at several other research questions, including:

* Whether the study drug can lower the level of α-synuclein protein in the Cerebrospinal Fluid (also referred to as "CSF", the fluid that surrounds the brain and spinal cord)

* How much study drug is in the blood, urine, and CSF at different times

* Compatible research to better understand the study drug (ALN-SNCA) and Parkinson's disease, including (but not limited to), whether the study drug can slow down the progression of Parkinson's disease symptoms

Who Is on the Research Team?

CT

Clinical Trial Management

Principal Investigator

Regeneron Pharmaceuticals

Are You a Good Fit for This Trial?

Inclusion Criteria

I have had Parkinson's disease for 4 years or less.
BMI ≤35 kg/m^2 at time of screening visit
I have Parkinson's disease with slow movement and at least one other main symptom.
See 1 more

Exclusion Criteria

I do not have any serious health conditions besides Parkinson's disease.
Any contraindications to undergo a brain Magnetic Resonance Imaging (MRI)
I have a bleeding disorder that increases my risk of bleeding.
See 5 more

What Are the Treatments Tested in This Trial?

Interventions

  • ALN-SNCA

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Placebo Group

Group I: ALN-SNCA Dose EscalationExperimental Treatment1 Intervention
Group II: Matching PlaceboPlacebo Group1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Regeneron Pharmaceuticals

Lead Sponsor

Trials
690
Recruited
948,000+
Founded
1988
Headquarters
Tarrytown, USA
Known For
Precision medicine
Top Products
Dupixent, EYLEA, Libtayo, Praluent
Leonard Schleifer profile image

Leonard Schleifer

Regeneron Pharmaceuticals

Chief Executive Officer since 1988

MD and PhD in Medicine

George Yancopoulos profile image

George Yancopoulos

Regeneron Pharmaceuticals

Chief Medical Officer since 1997

MD from Harvard Medical School