100 Participants Needed

Pacritinib for T-Cell Lymphoma

Recruiting at 5 trial locations
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial
Approved in 1 JurisdictionThis treatment is already approved in other countries

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial tests pacritinib, a drug that may benefit individuals with certain types of T-cell lymphoma, a cancer affecting the immune system. The main goal is to evaluate pacritinib's effectiveness for those whose cancer has returned or is not responding to previous treatments. Suitable participants have a confirmed diagnosis of a T-cell lymphoma type that is either relapsed (returned) or refractory (resistant to treatment) and are experiencing progression despite prior treatment. As a Phase 2 trial, this research focuses on assessing the treatment's effectiveness in an initial, smaller group of people.

Do I need to stop taking my current medications for the trial?

The trial requires a 2-week break from strong CYP3A4 inducers or inhibitors before starting the study drug. Also, medications that prolong QTc must be stopped within 5 half-lives before starting the trial. If you are on these medications, you may need to stop or adjust them.

Is there any evidence suggesting that pacritinib is likely to be safe for humans?

Research has shown that pacritinib is generally well-tolerated in people with certain recurring or hard-to-treat blood disorders. In earlier studies, common side effects included diarrhea, low platelet count (thrombocytopenia), nausea, low red blood cell count (anemia), and swelling from fluid retention (peripheral edema), occurring in 20% or more of patients.

The FDA has approved pacritinib for treating myelofibrosis, a different condition, which suggests it is somewhat safe. However, reports have noted lymphoma and other cancers, particularly in individuals who smoke or have smoked. Most patients managed these side effects with proper care.

Overall, while pacritinib has shown some side effects, its use in other conditions suggests it is relatively safe when monitored by a doctor.12345

Why do researchers think this study treatment might be promising for lymphoma?

Pacritinib is unique because it specifically targets the JAK2 and FLT3 pathways, which are often involved in the growth of T-cell lymphomas. Unlike traditional chemotherapy that broadly attacks fast-growing cells and might affect healthy cells, Pacritinib offers a more targeted approach, potentially reducing side effects. Researchers are excited about this treatment because it could provide a new option for patients with challenging subtypes of T-cell lymphoma, like PTCL, NOS, and AITL, that don't always respond well to existing therapies. Additionally, its oral administration offers a convenient alternative to intravenous treatments, making it easier for patients to adhere to their treatment regimen.

What evidence suggests that pacritinib might be an effective treatment for T-cell lymphoma?

Research has shown that pacritinib may help treat certain blood disorders. In earlier studies, over 80% of patients experienced symptom relief compared to those on other treatments. Pacritinib blocks signals in cancer cells that aid their survival and growth, making it potentially useful for conditions like T-cell lymphoma, where cancer cells depend on these signals. In this trial, participants will receive pacritinib as a single agent across different cohorts, each focusing on specific subtypes of T-cell lymphoma. Long-term treatment data suggest that most patients tolerate the treatment well. These findings support the idea that pacritinib could be a helpful option for those with relapsed or hard-to-treat blood disorders.14678

Who Is on the Research Team?

Ryan Alan Wilcox MD, PhD | Clinical ...

Ryan Wilcox, MD

Principal Investigator

University of Michigan Rogel Cancer Center

Are You a Good Fit for This Trial?

This trial is for adults with certain types of T-cell lymphoma that have not responded to previous treatments or have come back after treatment. Participants must be able to take pills, understand and comply with study procedures, and use effective contraception if necessary. They should not have severe psychiatric issues, gastrointestinal conditions affecting drug absorption, uncontrolled illnesses like heart disease or infections, nor should they be pregnant.

Inclusion Criteria

I can swallow pills without needing to break them down.
Ability to give informed consent
My disease came back or didn't respond to treatment within 6 months.
See 4 more

Exclusion Criteria

I don't have stomach or metabolic issues affecting medicine absorption.
I have not had major surgery in the last 3 weeks.
I have stopped taking medications that affect my heart's rhythm.
See 20 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Treatment

Patients receive single-agent treatment with pacritinib 200mg orally twice daily until any condition for treatment discontinuation has been met

Up to 2 years

Follow-up

Participants are monitored for safety and effectiveness after treatment

30 days post end of treatment

Long-term follow-up

Participants are monitored for long-term outcomes such as progression-free survival and duration of response

Up to approximately 5 years

What Are the Treatments Tested in This Trial?

Interventions

  • Pacritinib
Trial Overview The trial is testing the effectiveness of a medication called Pacritinib in patients who have relapsed (cancer has returned) or refractory (not responding to treatment) T-cell lymphoproliferative disorders. The focus is on how well this oral drug works against these specific types of cancer.
How Is the Trial Designed?
4Treatment groups
Experimental Treatment
Group I: Cohort 4: Less common PTCL subtypesExperimental Treatment1 Intervention
Group II: Cohort 3: CTCL (MF/SS)Experimental Treatment1 Intervention
Group III: Cohort 2: AITL/TFH PTCLExperimental Treatment1 Intervention
Group IV: Cohort 1: PTCL, NOSExperimental Treatment1 Intervention

Pacritinib is already approved in United States for the following indications:

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Approved in United States as Vonjo for:

Find a Clinic Near You

Who Is Running the Clinical Trial?

University of Michigan Rogel Cancer Center

Lead Sponsor

Trials
303
Recruited
20,700+

Hoosier Cancer Research Network

Collaborator

Trials
69
Recruited
3,800+

CTI BioPharma

Industry Sponsor

Trials
64
Recruited
5,400+

Dr. Adam R. Craig

CTI BioPharma

Chief Executive Officer since 2017

Member of the Royal College of Physicians (UK)

Dr. Monica Ravindra Shah

CTI BioPharma

Chief Medical Officer

MD from Brown Medical School

National Institutes of Health (NIH)

Collaborator

Trials
2,896
Recruited
8,053,000+

National Cancer Institute (NCI)

Collaborator

Trials
14,080
Recruited
41,180,000+

Published Research Related to This Trial

In a study of 1344 patients with peripheral T-cell lymphoma (PTCL), those treated with brentuximab vedotin plus cyclophosphamide, doxorubicin, and prednisone (A + CHP) had a lower rate of subsequent therapy compared to those treated with CHOP, indicating potentially better initial treatment efficacy.
The study highlighted that patients in the real-world setting were older and had more comorbidities than those in clinical trials, emphasizing the need for retrospective analyses to understand the impact of new treatments in diverse patient populations.
Retrospective Analysis With Propensity Score Matching of Peripheral T-Cell Lymphoma Treated Frontline With Brentuximab Vedotin and Chemotherapy.Burke, JM., Liu, N., Yu, KS., et al.[2023]
Peripheral T-cell lymphoma (PTCL) accounts for about 10% of non-Hodgkin lymphoma cases and includes 23 recognized subtypes, with patients often being more resistant to initial therapies compared to aggressive B-cell lymphomas.
For common nodal PTCL subtypes, anthracycline-based regimens followed by high-dose therapy and autologous stem cell transplantation (ASCT) in first chemosensitive remission yield the best outcomes, while several FDA-approved agents are available for relapsed or refractory cases.
Treatment of Peripheral T-Cell Lymphoma: Many Shades of Gray.Lunning, MA.[2015]
Alisertib (MLN8237), an oral Aurora A kinase inhibitor, has demonstrated the ability to reduce cell proliferation and induce apoptosis in various tumor cell lines, making it a promising treatment for aggressive peripheral T-cell lymphomas.
Currently undergoing Phase III trials, alisertib has shown single-agent antitumor activity in animal models and potential effectiveness in patients with relapsed or refractory peripheral T-cell lymphoma, highlighting its importance in developing new therapies for this challenging condition.
The role of alisertib in treatment of peripheral T-cell lymphomas.Gallop-Evans, E.[2015]

Citations

NCT04858256 | Pacritinib in Relapsed/Refractory T-cell ...The main purpose of this study is to determine the effectiveness of the study drug pacritinib in people with relapsed or refractory lymphoproliferative ...
2.vonjohcp.comvonjohcp.com/efficacy
VONJO® Efficacy DataMore than 80% of patients (plt <50 x 109/L) experienced any SVR on VONJO compared to over half of the patients on best available therapy (BAT) (83% vs 56%)*.
Long-term treatment with pacritinib on a compassionate ...In order to describe the long-term treatment experience with pacritinib, we analyzed data from 76 patients treated with pacritinib on a compassionate use basis ...
Pacritinib Effective in Patients With Intermediate-1 Risk ...An ad-hoc analysis of PERSIST trials found pacritinib improved spleen size and symptoms in INT-1 risk myelofibrosis, with good tolerability.
Pacritinib Effectively Inhibits Pro-Survival Signaling and ...Methods: We conducted comparative studies to evaluate the effects of pacritinib versus the covalent BTK-inhibitors ibrutinib and zanubrutinib on ...
6.vonjohcp.comvonjohcp.com/
VONJO® (pacritinib) HCP: VONJO® for Myelofibrosis TreatmentIn PERSIST-2, the most common adverse reactions in ≥20% of patients (n=106) were diarrhea, thrombocytopenia, nausea, anemia, and peripheral edema. Learn more ...
VONJO™ (pacritinib) capsules - accessdata.fda.govThe most common (≥20% of patients) adverse reactions are diarrhea, thrombocytopenia, nausea, anemia, and peripheral edema (6.1). To report ...
Data presented at ACR Convergence 2025 highlight ... - SobiLymphoma and other malignancies may occur. Past/current smokers may be at increased risk. Risk of Infection Delay starting VONJO until active ...
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