Susan L. Perlman, MD - Neurology ...

Dr. Susan Perlman, MD

Claim this profile

University of California - Los Angeles

Studies Friedreich Ataxia
Studies Spinocerebellar Ataxias
12 reported clinical trials
12 drugs studied

Affiliated Hospitals

Image of trial facility.

University Of California, Los Angeles

Image of trial facility.

UCLA Ataxia Center

Clinical Trials Susan Perlman, MD is currently running

Image of trial facility.

Natural History Study

for Friedreich Ataxia

This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and effective drugs and biological products for Friedreich ataxia.

Recruiting

1 award

N/A

6 criteria

Image of trial facility.

Omaveloxolone

for Friedreich's Ataxia

In this study, researchers will learn more about the safety of BIIB141, also known as omaveloxolone or SKYCLARYS®. This is a drug available for doctors to prescribe for people with Friedreich's Ataxia, also known as FA. This is known as an "observational" study, which collects health information about study participants without changing their medical care. Participants for this study will be found using a group called the Friedreich's Ataxia Global Clinical Consortium (FA GCC) UNIFIED Natural History Study (UNIFAI). The FA-GCC is a group of study research centers that helps provide clinical care for FA patients and also helps researchers learn more about how FA affects patients over a long time. The main objective of this study is to collect safety information in participants with FA from UNIFAI. Some of the participants in this study will be prescribed BIIB141 for the first time by their own doctors. Some of the participants will have started taking BIIB141 after joining UNIFAI, but less than 12 months before joining this study. The main questions researchers want to answer in this study are: * How many participants had serious adverse events (SAEs)? An adverse event is considered serious when it results in death, is life-threatening, causes lasting problems, or requires hospital care. * How many participants had adverse events (AEs) related to heart failure or liver damage caused by the drug? Researchers will also learn more about : • Why and when participants stopped treatment, left the study, or took more of the drug than was prescribed This study will be done as follows: * Participants will be screened to check if they can join the study. * After joining the study, the participants who had never started BIIB141 treatment before must start it within 6 months. Otherwise, all participants will take BIIB141 throughout this study as prescribed by their own doctor. * During the study, each participant's doctor will decide how often the participant visits the study research center to check on their health. This will be based on the doctor's own clinical judgment and what is recommended by the drug's label. * Data from the participants' regular visits to their doctor will be collected at 1 month, 2 months, 3 months, 6 months, 12 months, 24 months, 36 months, 48 months, and 60 months. * Each participant will be in the study for up to 5 years.

Recruiting

1 award

N/A

10 criteria

More about Susan Perlman, MD

Clinical Trial Related

5 years of experience running clinical trials · Led 12 trials as a Principal Investigator · 3 Active Clinical Trials

Treatments Susan Perlman, MD has experience with

  • Placebo
  • Observational Study
  • BIIB132
  • TAK-341
  • ONO-2808
  • Omaveloxolone

Other Doctors you might be interested in

Frequently asked questions

Do I need insurance to participate in a trial?

What does Susan Perlman, MD specialize in?

Is Susan Perlman, MD currently recruiting for clinical trials?

Are there any treatments that Susan Perlman, MD has studied deeply?

What is the best way to schedule an appointment with Susan Perlman, MD?

What is the office address of Susan Perlman, MD?

Is there any support for travel costs?