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Cyclodextrin
Trappsol Cyclo for Niemann-Pick Disease
Recruiting1 awardPhase 3
Salt Lake City, Utah
This trial is testing a medicine called Trappsol Cyclo, given through an IV, for patients with Niemann Pick disease type C1. The medicine helps remove harmful fat buildup in cells. The study will also look at safety in younger children. Trappsol Cyclo has shown promising results by mobilizing cholesterol, extending life, and reducing neurological damage in Niemann-Pick disease type C1.
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