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Gene Therapy
Gene Therapy for Duchenne Muscular Dystrophy
Recruiting1 awardPhase 3
Prairie Village, Kansas
This trial will test whether gene therapy is safe and effective for boys with Duchenne Muscular Dystrophy. Two thirds of participants will get the therapy, while the other third will get a placebo. Those in the placebo group will have the opportunity to get the therapy at the beginning of the second year.
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Get in touch with the study teamWe’ll send your responses to the study team and help you to setup your first screening. This is not the start of informed consent. Screening happens between you and the trial.